Discovery of small molecule CXCR4 antagonists

J Med Chem. 2007 Nov 15;50(23):5655-64. doi: 10.1021/jm070679i. Epub 2007 Oct 24.

Abstract

In light of a proposed molecular mechanism for the C-X-C chemokine receptor type 4 (CXCR4) antagonist 1 (AMD3100), a template with the general structure 2 was designed, and 15 was identified as a lead by means of an affinity binding assay against the ligand-mimicking CXCR4 antagonist 3 (TN14003). Following a structure-activity profile around 15, the design and synthesis of a series of novel small molecular CXCR4 antagonists led to the discovery of 32 (WZ811). The compound shows subnanomolar potency (EC50 = 0.3 nM) in an affinity binding assay. In addition, when subjected to in vitro functional evaluation, 32 efficiently inhibits CXCR4/stromal cell-derived factor-1 (SDF-1)-mediated modulation of cyclic adenosine monophophate (cAMP) levels (EC50 = 1.2 nM) and SDF-1 induced Matrigel invasion (EC50 = 5.2 nM). Molecular field topology analysis (MFTA), a 2D quantitative structure-activity relationship (QSAR) approach based on local molecular properties (Van der Waals radii (VdW), atomic charges, and local lipophilicity), applied to the 32 series suggests structural modifications to improve potency.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Aminopyridines / chemical synthesis*
  • Aminopyridines / chemistry
  • Aminopyridines / pharmacology
  • Antineoplastic Agents / chemical synthesis*
  • Antineoplastic Agents / chemistry
  • Antineoplastic Agents / pharmacology
  • Benzylamines / chemical synthesis*
  • Benzylamines / chemistry
  • Benzylamines / pharmacology
  • Binding, Competitive
  • Cell Line, Tumor
  • Chemokine CXCL12 / metabolism
  • Collagen
  • Cyclic AMP / metabolism
  • Drug Combinations
  • Fluorescence Resonance Energy Transfer
  • Humans
  • Laminin
  • Models, Molecular
  • Neoplasm Invasiveness
  • Proteoglycans
  • Quantitative Structure-Activity Relationship
  • Receptors, CXCR4 / antagonists & inhibitors*
  • Receptors, CXCR4 / chemistry
  • Stereoisomerism

Substances

  • Aminopyridines
  • Antineoplastic Agents
  • Benzylamines
  • Chemokine CXCL12
  • Drug Combinations
  • Laminin
  • N,N'-di-2-pyridinyl-1,4-benzenedimethanamine
  • Proteoglycans
  • Receptors, CXCR4
  • matrigel
  • Collagen
  • Cyclic AMP