Identification of the first synthetic steroidogenic factor 1 inverse agonists: pharmacological modulation of steroidogenic enzymes

Mol Pharmacol. 2008 Mar;73(3):900-8. doi: 10.1124/mol.107.040089. Epub 2007 Nov 30.

Abstract

Steroidogenic factor SF-1, a constitutively active nuclear hormone receptor, is essential to the development of adrenal and gonadal glands and acts as a shaping factor of sexual determination and differentiation. Its effects are exerted primarily through the control of the synthesis of steroid hormones. The functional cell-based assay Receptor Selection and Amplification Technology (R-SAT) was used to identify potent and selective SF-1 inverse agonists through the screening of a chemical library of drug-like small-molecule entities. Among them, 4-(heptyloxy)phenol (AC-45594), a prototype inverse agonist lead, was used to show that SF-1 constitutive activity can be pharmacologically modulated by a synthetic ligand. In a physiological system of endocrine function, the expression of several reported SF-1 target genes, including SF-1 itself, was inhibited by treatment with AC-45594 and analogs. Thus, pharmacological modulation of SF-1 is critical to its function as an endocrine master regulator and has potentially important consequences to diseases in which SF-1 activity is critical.

MeSH terms

  • Adrenal Gland Neoplasms / pathology
  • Animals
  • Carcinoma / pathology
  • Cell Proliferation / drug effects
  • Cholesterol Side-Chain Cleavage Enzyme / genetics*
  • Cholesterol Side-Chain Cleavage Enzyme / metabolism
  • Cyclic AMP / pharmacology
  • Drug Evaluation, Preclinical / methods*
  • Genes, Reporter
  • Humans
  • Inhibitory Concentration 50
  • Ligands
  • Luciferases / metabolism
  • Mice
  • Mutation
  • NIH 3T3 Cells
  • Phenols / pharmacology*
  • RNA, Messenger / metabolism
  • Steroidogenic Factor 1 / agonists*
  • Steroidogenic Factor 1 / chemical synthesis*
  • Steroidogenic Factor 1 / chemistry
  • Steroidogenic Factor 1 / genetics
  • Transcription, Genetic
  • Transcriptional Activation
  • Transfection
  • Tumor Cells, Cultured

Substances

  • 4-(heptyloxy)phenol
  • Ligands
  • Phenols
  • RNA, Messenger
  • Steroidogenic Factor 1
  • Cyclic AMP
  • Luciferases
  • Cholesterol Side-Chain Cleavage Enzyme