Treatment of pulmonary metastatic tumors in mice using lentiviral vector-engineered stem cells

Cancer Gene Ther. 2008 Feb;15(2):73-84. doi: 10.1038/sj.cgt.7701108. Epub 2007 Dec 14.

Abstract

Active cancer immunotherapy relies on functional tumor-specific effector T lymphocytes for tumor elimination. Dendritic cells (DCs), as most potent antigen-presenting cells, have been popularly employed in clinical and experimental tumor treatments. We have previously demonstrated that lentiviral vector-mediated transgene delivery to DC progenitors, including bone marrow cells and hematopoietic stem cells, followed by transplantation supports systemic generation of great numbers of tumor antigen-presenting DCs. These DCs subsequently stimulate marked and systemic immune activation. Here, we examined whether this level of immune activation is sufficient to overcome tumor-induced tolerogenic environment for treating an established aggressive epithelial tumor. We showed that a combination treatment of granulocyte macrophage-colony stimulating factor and cytosine-phosphate-guanine-containing oligonucleotide stimulated large numbers of tumor antigen-presenting DCs in situ from transgene-modified stem cells. Moreover, these in situ generated and activated DCs markedly stimulated activation of antigen-specific CD4 and CD8 T cells by augmenting their numbers, as well as function, even in a tumor-bearing tolerogenic environment. This leads to significant improvement in the therapeutic efficacy of established pulmonary metastases. This study suggests that lentiviral vector-modified stem cells as DC progenitors may be used as an effective therapeutic regimen for treating metastatic epithelial tumors.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Carcinoma, Renal Cell / secondary
  • Carcinoma, Renal Cell / therapy
  • Cell Line
  • Cell Line, Tumor
  • Dendritic Cells / metabolism
  • Dendritic Cells / transplantation
  • Female
  • Gene Transfer Techniques*
  • Genetic Therapy* / methods
  • Genetic Vectors*
  • Humans
  • Immunotherapy, Adoptive
  • Lentivirus / genetics*
  • Lung Neoplasms / secondary*
  • Lung Neoplasms / therapy*
  • Male
  • Mice
  • Mice, Inbred BALB C
  • Mice, Transgenic
  • Stem Cell Transplantation*
  • Stem Cells / metabolism*