BMS-214662 potently induces apoptosis of chronic myeloid leukemia stem and progenitor cells and synergizes with tyrosine kinase inhibitors

Blood. 2008 Mar 1;111(5):2843-53. doi: 10.1182/blood-2007-09-112573. Epub 2007 Dec 21.

Abstract

Chronic myeloid leukemia (CML), a hematopoietic stem-cell disorder, cannot be eradicated by conventional chemotherapy or the tyrosine kinase inhibitor imatinib mesylate (IM). To target CML stem/progenitor cells, we investigated BMS-214662, a cytotoxic farnesyltransferase inhibitor, previously reported to kill nonproliferating tumor cells. IM or dasatinib alone reversibly arrested proliferation of CML stem/progenitor cells without inducing apoptosis. In contrast, BMS-214662, alone or in combination with IM or dasatinib, potently induced apoptosis of both proliferating and quiescent CML stem/progenitor cells with less than 1% recovery of Philadelphia-positive long-term culture-initiating cells. Normal stem/progenitor cells were relatively spared by BMS-214662, suggesting selectivity for leukemic stem/progenitor cells. The ability to induce selective apoptosis of leukemic stem/progenitor cells was unique to BMS-214662 and not seen with a structurally similar agent BMS-225975. BMS-214662 was cytotoxic against CML blast crisis stem/progenitor cells, particularly in combination with a tyrosine kinase inhibitor and equally effective in cell lines harboring wild-type vs mutant BCR-ABL, including the T315I mutation. This is the first report of an agent with activity in resistant and blast crisis CML that selectively kills CML stem/progenitor cells through apoptosis and offers potential for eradication of chronic phase CML.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Antigens, CD34 / metabolism
  • Antineoplastic Agents / pharmacology
  • Apoptosis / drug effects*
  • Benzamides
  • Benzodiazepines / pharmacology*
  • Blast Crisis / pathology
  • Caspase 3 / metabolism
  • Cell Death / drug effects
  • Cell Survival / drug effects
  • Dasatinib
  • Drug Screening Assays, Antitumor
  • Drug Synergism
  • Farnesyltranstransferase / antagonists & inhibitors
  • Fusion Proteins, bcr-abl / chemistry
  • Fusion Proteins, bcr-abl / metabolism
  • Humans
  • Imatinib Mesylate
  • Imidazoles / pharmacology*
  • Leukemia, Myelogenous, Chronic, BCR-ABL Positive / enzymology
  • Leukemia, Myelogenous, Chronic, BCR-ABL Positive / pathology*
  • Mutation / genetics
  • Neoplastic Stem Cells / pathology*
  • Philadelphia Chromosome
  • Piperazines / pharmacology
  • Protein Kinase Inhibitors / pharmacology*
  • Protein Structure, Tertiary
  • Pyrimidines / pharmacology
  • Thiazoles / pharmacology

Substances

  • Antigens, CD34
  • Antineoplastic Agents
  • Benzamides
  • Imidazoles
  • Piperazines
  • Protein Kinase Inhibitors
  • Pyrimidines
  • Thiazoles
  • Benzodiazepines
  • Imatinib Mesylate
  • Farnesyltranstransferase
  • Fusion Proteins, bcr-abl
  • Caspase 3
  • 7-cyano-2,3,4,5-tetrahydro-1-(1H-imidazol-4-ylmethyl)-3-(phenylmethyl)-4-(2-thienylsulfonyl)-1H-1,4-benzodiazepine
  • Dasatinib