Identification and characterization of the first large deletion of the MYH9 gene associated with MYH9 disorders

Eur J Haematol. 2008 Jun;80(6):540-4. doi: 10.1111/j.1600-0609.2008.01046.x. Epub 2008 Feb 13.

Abstract

MYH9 disorders are autosomal dominant macrothrombocytopenias with leukocyte inclusion bodies. Single point mutations in the protein-coding sequence of the MYH9 gene are the most common cause. So far no large gene deletion/insertion and splicing defects have been reported. Conventional DNA sequencing of each MYH9-coding exon showed no abnormalities in a patient. Reverse transcription- polymerase chain reaction (PCR) amplification and sequencing of neutrophil mRNA identified an inframe deletion of exon 25. Further long-range PCR amplification of genomic DNA revealed a deletion of 1220 nucleotides including entire exon 25. Immunoblot analysis showed a small, abnormal protein in neutrophils but not in platelets. This is the first report of a large deletion of the MYH9 gene leading to the development of MYH9 disorders.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Base Sequence
  • Blotting, Western
  • DNA Primers
  • Gene Deletion*
  • Humans
  • Male
  • Molecular Motor Proteins / genetics*
  • Myosin Heavy Chains / genetics*
  • Thrombocytopenia / genetics*

Substances

  • DNA Primers
  • MYH9 protein, human
  • Molecular Motor Proteins
  • Myosin Heavy Chains