Mobilization of PML-RARA negative blood stem cells and salvage with autologous peripheral blood stem cell transplantation in children with relapsed acute promyelocytic leukemia

Pediatr Blood Cancer. 2008 Oct;51(4):521-4. doi: 10.1002/pbc.21614.

Abstract

Background: Relapsed acute promyleocytic leukemia (APL) is treated with re-induction chemotherapy, commonly arsenic trioxide, and stem cell transplantation (SCT). The effect of arsenic trioxide on autologous peripheral blood stem cell collection is unknown.

Procedure: Five pediatric patients with relapsed APL had PML-RARA negative peripheral blood stem cells mobilized (four after arsenic trioxide) and underwent autologous SCT after cyclophosphamide (60 mg/kg x 2) and total body irradiation (TBI-fractionated 1,200 cGy) conditioning.

Results: All five patients remain in molecular remission a median of 20 months post-transplant.

Conclusion: Autologous SCT performed during molecular remission is a treatment option for pediatric patients with relapsed APL and may provide durable leukemia-free survival without the complications of allogeneic transplantation.

MeSH terms

  • Adolescent
  • Child
  • Child, Preschool
  • Graft Survival
  • Hematopoietic Stem Cells / metabolism*
  • Humans
  • Leukemia, Promyelocytic, Acute / metabolism
  • Leukemia, Promyelocytic, Acute / surgery*
  • Oncogene Proteins, Fusion / metabolism
  • Peripheral Blood Stem Cell Transplantation* / adverse effects
  • Recurrence
  • Salvage Therapy
  • Transplantation, Autologous / adverse effects

Substances

  • Oncogene Proteins, Fusion
  • promyelocytic leukemia-retinoic acid receptor alpha fusion oncoprotein