Syndromic congenital sensorineural deafness, microtia and microdontia resulting from a novel homoallelic mutation in fibroblast growth factor 3 (FGF3)

Eur J Hum Genet. 2009 Jan;17(1):14-21. doi: 10.1038/ejhg.2008.141. Epub 2008 Aug 13.

Abstract

We identified a homozygous missense mutation (c.196G-->T) in fibroblast growth factor 3 (FGF3) in 21 affected individuals from a large extended consanguineous Saudi family, phenotypically characterized by autosomal recessive syndromic congenital sensorineural deafness, microtia and microdontia. All affected family members are descendents of a common ancestor who had lived six generations ago in a geographically isolated small village. This is the second report of FGF3 involvement in syndromic deafness in humans, and independently confirms the gene's positive role in inner ear development. The c.196G-->T mutation results in substitution of glycine by cysteine at amino acid 66 (p.G66C). This residue is conserved in several species and across 18 FGF family members. Conserved glycine/proline residues are central to the 'beta-trefoil fold' characteristic of the secondary structure of FGF family proteins and substitution of these residues is likely to disrupt structure and consequently function.

MeSH terms

  • Abnormalities, Multiple / genetics*
  • Adolescent
  • Adult
  • Amino Acid Substitution
  • Child
  • Child, Preschool
  • Chromosome Mapping
  • Consanguinity
  • Deafness / genetics*
  • Ear, External / abnormalities*
  • Ear, Inner / abnormalities*
  • Female
  • Fibroblast Growth Factor 3 / chemistry
  • Fibroblast Growth Factor 3 / genetics*
  • Fibroblast Growth Factor 3 / physiology
  • Hearing Loss, Sensorineural / genetics*
  • Humans
  • Infant
  • Male
  • Middle Aged
  • Mutation, Missense
  • Pedigree
  • Syndrome
  • Tooth Abnormalities / genetics*
  • Young Adult

Substances

  • FGF3 protein, human
  • Fibroblast Growth Factor 3