RNA interference of Trypanosoma brucei cathepsin B and L affects disease progression in a mouse model

PLoS Negl Trop Dis. 2008 Sep 24;2(9):e298. doi: 10.1371/journal.pntd.0000298.

Abstract

We investigated the roles played by the cysteine proteases cathepsin B and cathepsin L (brucipain) in the pathogenesis of Trypansoma brucei brucei in both an in vivo mouse model and an in vitro model of the blood-brain barrier. Doxycycline induction of RNAi targeting cathepsin B led to parasite clearance from the bloodstream and prevent a lethal infection in the mice. In contrast, all mice infected with T. brucei containing the uninduced Trypanosoma brucei cathepsin B (TbCatB) RNA construct died by day 13. Induction of RNAi against brucipain did not cure mice from infection; however, 50% of these mice survived 60 days longer than uninduced controls. The ability of T. b. brucei to cross an in vitro model of the human blood-brain barrier was also reduced by brucipain RNAi induction. Taken together, the data suggest that while TbCatB is the more likely target for the development of new chemotherapy, a possible role for brucipain is in facilitating parasite entry into the brain.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Cathepsin B / genetics*
  • Cathepsin L / genetics*
  • Cysteine Endopeptidases / genetics
  • Cysteine Endopeptidases / metabolism
  • Genes, Reporter
  • Humans
  • Life Cycle Stages / genetics
  • Life Cycle Stages / physiology
  • Mice
  • Models, Animal
  • Plasmids
  • Protozoan Proteins / genetics
  • Protozoan Proteins / metabolism
  • RNA Interference* / drug effects
  • Reverse Transcriptase Polymerase Chain Reaction
  • Tetracycline / pharmacology
  • Transfection
  • Trypanosoma brucei brucei / enzymology*
  • Trypanosoma brucei brucei / genetics*
  • Trypanosoma brucei brucei / physiology
  • Trypanosomiasis, African

Substances

  • Protozoan Proteins
  • Cysteine Endopeptidases
  • trypanopain Tb
  • Cathepsin B
  • Cathepsin L
  • Tetracycline