Long-term response of juvenile idiopathic arthritis after conditioning with 8 Gy total body irradiation followed by autologous peripheral blood stem cells: case report

Pediatr Transplant. 2010 Sep 1;14(6):E65-9. doi: 10.1111/j.1399-3046.2009.01129.x. Epub 2009 Feb 20.

Abstract

Investigations of HCT for refractory JIA have employed high dose immunosuppressive drugs, such as CY and ATG with or without low dose TBI. Initial disease response has been observed in approximately two-thirds of patients; however, relapse occurs in about half of the responders. The current report describes a regimen with substantially increased dose of TBI, previously shown to be associated with high rate of disease response in adult patients with refractory MS and severe SSc. We report outcome of the lead patient in this pilot study, who remains in complete remission now, five yr after HCT. This regimen should be considered for patients with JIA refractory to medical therapies, including previous low intensity regimen HCT.

Publication types

  • Case Reports
  • Multicenter Study
  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Arthritis, Juvenile / drug therapy
  • Arthritis, Juvenile / immunology
  • Arthritis, Juvenile / radiotherapy
  • Arthritis, Juvenile / surgery*
  • Drug Therapy, Combination
  • Humans
  • Immunosuppressive Agents / administration & dosage
  • Male
  • Patient Selection
  • Peripheral Blood Stem Cell Transplantation* / methods
  • Radiotherapy Dosage
  • Transplantation Conditioning
  • Treatment Outcome
  • Whole-Body Irradiation

Substances

  • Immunosuppressive Agents