Iron overload and chelation therapy in patients with low-risk myelodysplastic syndromes with transfusion requirements

Ann Hematol. 2010 Feb;89(2):147-54. doi: 10.1007/s00277-009-0794-7. Epub 2009 Aug 19.

Abstract

The main objective of the study was to analyze the incidence of iron overload (IO) and its management in transfusion-dependent patients with low-risk myelodysplastic syndrome (MDS) before the license of deferasirox. This observational, cross-sectional, and multicenter study was conducted from January to May 2007 in 81 Spanish hospitals. Eligible patients had a low or intermediate-1 risk score and had to have received at least ten units of packed red blood cell (PRBC). Of the 549 patients analyzed, 75% had received more than 20 PRBC units since diagnosis; 14% had IO at diagnosis and 58% at last follow-up. Thirty-eight percent of patients received chelation therapy; of those, 92% were treated with desferrioxamine. Ferritin levels at the start of chelation therapy were higher than 1,000 microg/L in 76% and over 2,500 microg/L in 24% of patients. Of the 202 patients who received some form of chelation therapy, ferritin levels increased from a mean +/- SD of 1,986 +/- 1,398 to 2,480 +/- 1,648 microg/L at last follow-up in 86% (p < 0.001). In the remaining 29 patients treated with a minimally effective therapy, ferritin levels did not increase. Of these, only 11 patients received such therapy lasting more than 12 months. In conclusion, most low-risk transfusion-dependent MDS patients develop IO, but only a minority receives a minimally effective and timely iron chelation therapy.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Aged
  • Aged, 80 and over
  • Benzoates / therapeutic use
  • Chelation Therapy*
  • Deferasirox
  • Deferoxamine / therapeutic use
  • Erythrocyte Transfusion*
  • Female
  • Ferritins / blood
  • Humans
  • Iron Chelating Agents / therapeutic use*
  • Iron Overload / diagnosis
  • Iron Overload / drug therapy*
  • Male
  • Middle Aged
  • Multicenter Studies as Topic
  • Myelodysplastic Syndromes / blood
  • Myelodysplastic Syndromes / physiopathology
  • Myelodysplastic Syndromes / therapy*
  • Triazoles / therapeutic use

Substances

  • Benzoates
  • Iron Chelating Agents
  • Triazoles
  • Ferritins
  • Deferoxamine
  • Deferasirox