Irrespective of CD34 expression, lineage-committed cell fraction reconstitutes and re-establishes transformed Philadelphia chromosome-positive leukemia in NOD/SCID/IL-2Rgammac-/- mice

Cancer Sci. 2010 Mar;101(3):631-8. doi: 10.1111/j.1349-7006.2009.01440.x. Epub 2009 Nov 16.

Abstract

Stem cells of acute myeloid leukemia (AML) have been identified as immunodeficient mouse-repopulating cells with a Lin(-)CD34(+)38(-) phenotype similar to normal hematopoietic stem cells. To identify the leukemia-propagating stem cell fraction of Philadelphia chromosome-positive (Ph(+)) leukemia, we serially transplanted human leukemia cells from patients with chronic myeloid leukemia blast crisis (n = 3) or Ph(+) acute lymphoblastic leukemia (n = 3) into NOD/SCID/IL-2Rgammac(-/-) mice. Engrafted cells were almost identical to the original leukemia cells as to phenotypes, IGH rearrangements, and karyotypes. CD34(+)CD38(-)CD19(+), CD34(+)38(+)CD19(+), and CD34(-)CD38(+)CD19(+) fractions could self-renew and transfer the leukemia, whereas the CD34(-)CD38(+)CD19(+) fraction did not stably propagate in NOD/SCID mice. These findings suggest that leukemia-repopulating cells in transformed Ph(+) leukemia are included in a lineage-committed but multilayered fraction, and that CD34(+) leukemia cells potentially emerge from CD34(-) populations.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • ADP-ribosyl Cyclase 1 / analysis
  • Animals
  • Antigens, CD34 / analysis
  • Antigens, CD34 / physiology*
  • Cell Lineage*
  • Humans
  • Leukemia / genetics
  • Leukemia / pathology*
  • Mice
  • Mice, Inbred NOD
  • Mice, SCID
  • Philadelphia Chromosome*
  • Receptors, Interleukin-2 / physiology*

Substances

  • Antigens, CD34
  • Receptors, Interleukin-2
  • ADP-ribosyl Cyclase 1