Discontinuation of growth hormone (GH) treatment during the transition phase is an important factor determining the phenotype of young adults with nonidiopathic childhood-onset GH deficiency

J Clin Endocrinol Metab. 2010 Jun;95(6):2646-54. doi: 10.1210/jc.2009-2013. Epub 2010 Mar 24.

Abstract

Context: Little is known about the impact of childhood-onset GH deficiency (GHD), in particular the duration of GH cessation during the transition phase, on adult phenotype.

Objective: We investigated the association between the manifestations and management of GHD during childhood/adolescence and the clinical features of GHD in adulthood. DESIGN/SETTING/PATIENTS/INTERVENTION: Patients with reconfirmed childhood-onset GHD who resumed GH treatment as adults were identified from two sequential databases (n = 313). The cohort was followed up longitudinally from GH start in childhood to reinitiation of treatment in adulthood and 1 yr beyond. Analyses were performed in the total cohort and in subgroups of patients with idiopathic GHD (IGHD) and non-IGHD. The cohorts were stratified based on duration of GH cessation (short, < or = 2 yr; long, > 2 yr).

Main outcome measures: Regimen of pediatric GH administration, duration of GH interruption, IGF-I sd score, lipid concentrations, and quality of life were measured.

Results: Mean duration of GH interruption was 4.4 yr. IGF-I sd score in adulthood was related to severity of childhood GHD. In non-IGHD patients, a longer duration of GH interruption was associated with a worse lipid profile (P < 0.0001). Non-IGHD patients who gained more height during childhood GH treatment reported better quality of life than those who gained less height (P < 0.05).

Conclusions: Pediatricians should tailor GH treatment, not only for its beneficial effect on growth but also for future health in adulthood. In adults with reconfirmed GHD, particularly those with non-IGHD, early recommencement of GH should be considered.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Aging / physiology
  • Body Height / drug effects
  • Body Height / physiology
  • Body Mass Index
  • Child
  • Cohort Studies
  • Craniopharyngioma / blood
  • Craniopharyngioma / complications
  • Female
  • Growth / drug effects
  • Growth / physiology*
  • Human Growth Hormone / administration & dosage
  • Human Growth Hormone / therapeutic use*
  • Humans
  • Insulin-Like Growth Factor I / metabolism
  • Lipid Metabolism / physiology
  • Lipids / blood
  • Longitudinal Studies
  • Male
  • Patient Selection
  • Phenotype
  • Pituitary Neoplasms / blood
  • Pituitary Neoplasms / complications
  • Quality of Life
  • Recombinant Proteins / administration & dosage
  • Recombinant Proteins / therapeutic use
  • Regression Analysis
  • Treatment Outcome

Substances

  • Lipids
  • Recombinant Proteins
  • Human Growth Hormone
  • Insulin-Like Growth Factor I