[Niemann-Pick type C disease: an early diagnosis for a therapeutic hope]

Arch Pediatr. 2010 Jun:17 Suppl 2:S39-40. doi: 10.1016/S0929-693X(10)70009-9.
[Article in French]
No abstract available

MeSH terms

  • Early Diagnosis
  • Genetic Therapy
  • Humans
  • Niemann-Pick Disease, Type C / diagnosis*
  • Niemann-Pick Disease, Type C / therapy
  • beta-Cyclodextrins

Substances

  • beta-Cyclodextrins