Novel reduction-responsive cross-linked polyethylenimine derivatives by click chemistry for nonviral gene delivery

Bioconjug Chem. 2010 Oct 20;21(10):1827-35. doi: 10.1021/bc100191r.

Abstract

Novel reducible disulfide-containing cross-linked polyethylenimines (PEI-SS-CLs) were synthesized via click chemistry and evaluated as nonviral gene delivery vectors. First, about four azide pendant groups were introduced into a low-molecular-weight (LMW) PEI (1.8 kDa) to get an azide-terminated PEI. Then, click reaction between a disulfide-containing dialkyne cross-linker and the azide functionalized LMW PEI resulted in a high-molecular-weight disulfide-containing cross-linked PEI composed of LMW constitute via a reducible cross-linker. The synthesized polymers were characterized by (1)H NMR, FTIR, and size-exclusion chromatography (SEC). It was shown that the obtained disulfide-containing cross-linked PEIs were able to condense plasmid DNA into positively charged nanoparticles. The degradation of the disulfide cross-linked polymers PEI-SS-CLs induced by DTT was confirmed by a gel retardation assay and SEC analysis. In vitro experiments revealed that the reducible PEI-SS-CLs were less cytotoxic and more effective in gene transfection (in both the presence and absence of serum) than the control nondegradable 25-kDa PEI. This study demonstrates that a reducibly degradable cationic polymer composed of LMW PEI cross-linked via a disulfide-containing linker possesses both higher gene transfection efficiency and lower cytotoxicity than PEI (25 kDa). These polymers are therefore attractive candidates for further in vivo evaluations.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Alkynes / chemistry
  • Azides / chemistry
  • Click Chemistry*
  • Disulfides / chemistry
  • Drug Carriers / chemistry*
  • Drug Carriers / metabolism*
  • Drug Carriers / toxicity
  • HEK293 Cells
  • HeLa Cells
  • Humans
  • Molecular Weight
  • Oxidation-Reduction
  • Polyethyleneimine / chemistry*
  • Transfection / methods*

Substances

  • Alkynes
  • Azides
  • Disulfides
  • Drug Carriers
  • Polyethyleneimine