FLNA p.V528M substitution is neither associated with bilateral periventricular nodular heterotopia nor with macrothrombocytopenia

J Hum Genet. 2010 Dec;55(12):844-6. doi: 10.1038/jhg.2010.114. Epub 2010 Sep 16.

Abstract

Filamin A is encoded by the FLNA gene on chromosome Xq28 and functions in cross-linking actin filaments into orthogonal networks in the cortical cytoplasm. FLNA p.V528M was initially detected in a female autopsy case of X-linked bilateral periventricular nodular heterotopia (BPNH), a neuronal migration disorder characterized by subependymal nodules of gray matter. During our mutation analysis of FLNA in a boy with apparent X-linked thrombocytopenia, we detected the p.V528M variant. The patient, mother and sister, who were heterozygous for the substitution, did not have BPNH. We observed an allele frequency of 4.8% in healthy control Japanese, but did not observe the variant in Caucasian subjects. Hemizygous controls had a normal platelet count and size. We suggest that p.V528M is neither associated with BPNH nor with thrombocytopenia and giant platelets, and represents a functional polymorphism.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Amino Acid Substitution
  • Bernard-Soulier Syndrome / genetics*
  • Child
  • Child, Preschool
  • Contractile Proteins / genetics*
  • DNA Mutational Analysis
  • Female
  • Filamins
  • Gene Frequency
  • Genetic Diseases, X-Linked / genetics*
  • Humans
  • Male
  • Microfilament Proteins / genetics*
  • Pedigree
  • Periventricular Nodular Heterotopia / genetics*
  • Thrombocytopenia / genetics*

Substances

  • Contractile Proteins
  • Filamins
  • Microfilament Proteins