Characterization and mechanistic studies of a novel melanoma-targeting construct containing IκBa for specific inhibition of nuclear factor-κB activity

Neoplasia. 2010 Oct;12(10):766-77. doi: 10.1593/neo.10214.

Abstract

The transcription factor nuclear factor-κB (NF-κB) is a central mediator of growth and homeostasis for both normal and neoplastic cells. IκBα is the natural intracellular inhibitor of NF-κB and can effectively complex with and thereby inhibit the biologic activity and translocation of NF-κB to the nucleus. We designed a fusion protein designated IκBα/scFvMEL composing of human IκBα and the single-chain antibody scFvMEL, targets melanoma gp240 antigen. Cells treated with IκBα/scFvMEL before irradiation showed specifically inhibition of both constitutive and radiation-induced NF-κB activity on gp240 antigen-positive A375M cells. Pretreatment of A375M cells with IκBα/scFvMEL significantly sensitized melanoma cells to ionizing radiation assessed using a clonogenic survival assay. Mechanistic studies showed that IκBα/scFvMEL, when exogenously added to A375M cells, could be coimmunoprecipitated with the p65 subunit of NF-κB. IκBα/scFvMEL inhibited in a time and/or dose-dependent manner of tumor necrosis factor α- or radiation-induced NF-κB activity in vitro. IκBα/scFvMEL was also shown to specifically inhibit the translocation of the NF-κB p65 subunit to the cell nucleus and NF-κB-mediated gene transcription. Further, initial studies showed that mice bearing well-established A375M xenografts were treated (intravenously) with IκBα/scFvMEL and showed a significant suppression of tumor growth. We also observed a decrease in levels of Bcl-2 and Bcl-XL signaling events downstream of NF-κB in the tumor model. These studies demonstrate for the first time that tumor cell-targeted delivery of IκBα may be beneficial for the treatment of melanoma when combined with standard anticancer therapies such as radiation.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Apoptosis
  • Blotting, Western
  • Cell Nucleus / genetics
  • Cell Nucleus / metabolism
  • Cell Nucleus / radiation effects
  • Dose-Response Relationship, Drug
  • Electrophoretic Mobility Shift Assay
  • Enzyme-Linked Immunosorbent Assay
  • Flow Cytometry
  • Humans
  • I-kappa B Proteins / therapeutic use*
  • Immunoenzyme Techniques
  • Melanoma, Experimental / genetics
  • Melanoma, Experimental / pathology
  • Melanoma, Experimental / therapy*
  • Mice
  • Mice, Nude
  • NF-KappaB Inhibitor alpha
  • NF-kappa B / antagonists & inhibitors*
  • Phosphorylation
  • Protein Transport / radiation effects
  • Proteoglycans / immunology*
  • RNA, Messenger / genetics
  • Radiation, Ionizing
  • Radiation-Sensitizing Agents / pharmacology*
  • Recombinant Fusion Proteins / therapeutic use*
  • Reverse Transcriptase Polymerase Chain Reaction
  • Signal Transduction / radiation effects
  • Single-Chain Antibodies / therapeutic use*
  • Transcription Factor RelA / metabolism
  • Tumor Necrosis Factor-alpha / pharmacology

Substances

  • I-kappa B Proteins
  • NF-kappa B
  • NFKBIA protein, human
  • Nfkbia protein, mouse
  • Proteoglycans
  • RNA, Messenger
  • Radiation-Sensitizing Agents
  • Recombinant Fusion Proteins
  • Rela protein, mouse
  • Single-Chain Antibodies
  • Transcription Factor RelA
  • Tumor Necrosis Factor-alpha
  • gp240 glycoprotein, human
  • NF-KappaB Inhibitor alpha