A unique presentation of Wiskott-Aldrich syndrome in relation to platelet size

Pediatr Blood Cancer. 2011 Jul 1;56(7):1127-9. doi: 10.1002/pbc.22920. Epub 2011 Feb 10.

Abstract

Wiskott-Aldrich Syndrome (WAS) is a triad of immunodeficiency, eczema, and thrombocytopenia. Despite the heterogeneity of genetic and clinical findings, a correlation with small platelet size is routinely observed. Herein we describe a case with a unique phenotype that links normal mean platelet volume with the classic characteristics of this disease. The diagnosis was verified by genetic analysis showing a novel and de novo mutation. Our case illustrates that a high index of suspicion of WAS is warranted even in the setting of normal sized platelets.

Publication types

  • Case Reports

MeSH terms

  • Blood Platelets*
  • Cell Size
  • Humans
  • Infant
  • Male
  • Mutation / genetics
  • Phenotype
  • Platelet Count
  • Thrombocytopenia / diagnosis*
  • Thrombocytopenia / genetics
  • Thrombocytopenia / therapy
  • Treatment Outcome
  • Wiskott-Aldrich Syndrome / diagnosis*
  • Wiskott-Aldrich Syndrome / genetics
  • Wiskott-Aldrich Syndrome / therapy
  • Wiskott-Aldrich Syndrome Protein / genetics

Substances

  • Wiskott-Aldrich Syndrome Protein