Revealing a steroid receptor ligand as a unique PPARγ agonist

Cell Res. 2012 Apr;22(4):746-56. doi: 10.1038/cr.2011.162. Epub 2011 Oct 11.

Abstract

Peroxisome proliferator-activated receptor gamma (PPARγ) regulates metabolic homeostasis and is a molecular target for anti-diabetic drugs. We report here the identification of a steroid receptor ligand, RU-486, as an unexpected PPARγ agonist, thereby uncovering a novel signaling route for this steroid drug. Similar to rosiglitazone, RU-486 modulates the expression of key PPARγ target genes and promotes adipocyte differentiation, but with a lower adipogenic activity. Structural and functional studies of receptor-ligand interactions reveal the molecular basis for a unique binding mode for RU-486 in the PPARγ ligand-binding pocket with distinctive properties and epitopes, providing the molecular mechanisms for the discrimination of RU-486 from thiazolidinediones (TZDs) drugs. Our findings together indicate that steroid compounds may represent an alternative approach for designing non-TZD PPARγ ligands in the treatment of insulin resistance.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, Non-P.H.S.

MeSH terms

  • Adipocytes / drug effects
  • Adipocytes / metabolism
  • Adipogenesis / drug effects
  • Animals
  • Binding Sites
  • COS Cells
  • Chlorocebus aethiops
  • Gene Expression Regulation / drug effects*
  • Humans
  • Ligands
  • Mifepristone / chemistry*
  • Mifepristone / pharmacology*
  • Nuclear Receptor Coactivators / agonists
  • Nuclear Receptor Coactivators / chemistry*
  • Nuclear Receptor Coactivators / genetics*
  • Protein Binding
  • Protein Conformation
  • Protein Structure, Tertiary
  • Signal Transduction
  • Structure-Activity Relationship
  • Thiazolidinediones / chemistry

Substances

  • Ligands
  • NCOA6 protein, human
  • Nuclear Receptor Coactivators
  • Thiazolidinediones
  • Mifepristone

Associated data

  • PDB/3QT0