Structure-activity relationships in toll-like receptor 2-agonists leading to simplified monoacyl lipopeptides

J Med Chem. 2011 Dec 8;54(23):8148-60. doi: 10.1021/jm201071e. Epub 2011 Nov 4.

Abstract

Toll-like receptor 2-agonistic lipopeptides typified by S-[2,3-bis(palmitoyloxy)-(2RS)-propyl]-R-cysteinyl-S-serine (PAM(2)CS) compounds are potential vaccine adjuvants. In continuation of previously reported structure-activity relationships on this chemotype, we have determined that at least one acyl group of optimal length (C(16)) and an appropriately oriented ester carbonyl group is essential for TLR2-agonistic activity. The spacing between one of the palmitoyl ester carbonyl and the thioether is crucial to allow for an important H-bond, which observed in the crystal structure of the lipopeptide:TLR2 complex; consequently, activity is lost in homologated compounds. Penicillamine-derived analogues are also inactive, likely due to unfavorable steric interactions with the carbonyl of Ser 12 in TLR2. The thioether in this chemotype can be replaced with a selenoether. Importantly, the thioglycerol motif can be dispensed with altogether and can be replaced with a thioethanol bridge. These results have led to a structurally simpler, synthetically more accessible, and water-soluble analogue possessing strong TLR2-agonistic activities in human blood.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • Adjuvants, Immunologic / chemical synthesis*
  • Adjuvants, Immunologic / pharmacology
  • Animals
  • Humans
  • Linoleic Acids / chemical synthesis
  • Linoleic Acids / immunology
  • Linoleic Acids / pharmacology
  • Lipopeptides / chemical synthesis*
  • Lipopeptides / immunology
  • Lipopeptides / pharmacology
  • Mice
  • Models, Molecular
  • Molecular Structure
  • Solubility
  • Stereoisomerism
  • Structure-Activity Relationship
  • Toll-Like Receptor 2 / agonists*
  • alpha-Linolenic Acid / analogs & derivatives
  • alpha-Linolenic Acid / chemical synthesis
  • alpha-Linolenic Acid / immunology
  • alpha-Linolenic Acid / pharmacology

Substances

  • Adjuvants, Immunologic
  • Linoleic Acids
  • Lipopeptides
  • Toll-Like Receptor 2
  • alpha-Linolenic Acid