Gene therapy strategies for Usher syndrome type 1B

Adv Exp Med Biol. 2012:723:235-42. doi: 10.1007/978-1-4614-0631-0_31.
No abstract available

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't
  • Review

MeSH terms

  • Animals
  • Dependovirus / genetics*
  • Genetic Therapy / methods*
  • Humans
  • Lentivirus / genetics*
  • Mice
  • Myosin VIIa
  • Myosins / genetics*
  • Opsins / genetics
  • Usher Syndromes / genetics*
  • Usher Syndromes / pathology
  • Usher Syndromes / therapy*

Substances

  • MYO7A protein, human
  • Myo7a protein, mouse
  • Myosin VIIa
  • Opsins
  • Myosins

Supplementary concepts

  • Usher syndrome, type 1B