Relationship between neonatal screening results by HPLC and the number of α-thalassaemia gene mutations; consequences for the cut-off value

J Med Screen. 2011;18(4):182-6. doi: 10.1258/jms.2011.011043.

Abstract

Objectives: To evaluate the relationship between FAST peak percentage by adapted Bio-Rad Vnbs analysis using the valley-to-valley integration and genotypes with the aim to improve differentiation between severe α-thalassaemia forms (HbH disease) and the milder disease types.

Method: DNA analysis for α-thalassaemia was performed on 91 dried blood spot samples presenting normal and elevated FAST peak levels, selected during three years of Dutch national newborn screening.

Results: Significant differences were found between samples with and without α-thalassaemia mutations, regardless of the genetic profiles. No significant difference was demonstrated between HPLC in -α/αα and -α/-α, between -α/-α and - -/αα and between - -/αα and - -/-α genotypes.

Conclusion: This study confirms that the percentage HbBart's, as depicted by the FAST peak, is only a relative indication for the number of α genes affected in α-thalassaemia. Based on the data obtained using the modified Bio-Rad Vnbs software, we adopted a cut-off value of 22.5% to discriminate between possible severe α-thalassaemia or HbH disease and other α-thalassaemia phenotypes. Retrospectively, if this cut-off value was utilized during this initial three-year period of neonatal screening, the positive predictive value would have been 0.030 instead of 0.014.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Blood Chemical Analysis / methods
  • Chromatography, High Pressure Liquid
  • DNA Mutational Analysis
  • Fetal Blood / chemistry
  • Genetic Testing / methods*
  • Hemoglobin H / analysis
  • Hemoglobin H / genetics
  • Hemoglobins, Abnormal / analysis
  • Hemoglobins, Abnormal / genetics
  • Heterozygote
  • Homozygote
  • Humans
  • Infant, Newborn
  • Mutation*
  • Neonatal Screening / methods*
  • Netherlands
  • Retrospective Studies
  • alpha-Globins / analysis
  • alpha-Globins / genetics
  • alpha-Thalassemia / blood
  • alpha-Thalassemia / diagnosis*
  • alpha-Thalassemia / genetics*

Substances

  • Hemoglobins, Abnormal
  • alpha-Globins
  • Hemoglobin H
  • hemoglobin Bart's