Self-complementary AAVs induce more potent transgene product-specific immune responses compared to a single-stranded genome

Mol Ther. 2012 Mar;20(3):572-9. doi: 10.1038/mt.2011.280. Epub 2011 Dec 20.

Abstract

Using a mouse model we show that self-complementary (sc) adeno-associated virus (AAV) vectors pseudotyped with capsids of serotypes 2, 7 or 8 induce more potent transgene product-specific CD8(+) T cell and antibody responses compared to corresponding single-stranded (ss)AAV vectors. These data suggest that the higher and more rapidly appearing amounts of transgene product achieved with scAAV vectors may increase detrimental immune responses in gene transfer recipients.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • Animals
  • Antibodies, Viral / immunology
  • CD8-Positive T-Lymphocytes / immunology
  • CD8-Positive T-Lymphocytes / metabolism
  • Cytokines / biosynthesis
  • Dependovirus / genetics*
  • Dependovirus / immunology
  • Female
  • Gene Transfer Techniques
  • Genetic Vectors / genetics*
  • Genetic Vectors / immunology
  • Genome, Viral*
  • Immunophenotyping
  • Kinetics
  • Mice
  • Mice, Inbred BALB C
  • Transgenes / immunology*
  • gag Gene Products, Human Immunodeficiency Virus / genetics
  • gag Gene Products, Human Immunodeficiency Virus / immunology

Substances

  • Antibodies, Viral
  • Cytokines
  • gag Gene Products, Human Immunodeficiency Virus