Gene therapy for Fanconi anemia: one step closer to the clinic

Hum Gene Ther. 2012 Feb;23(2):141-4. doi: 10.1089/hum.2011.237.
No abstract available

Publication types

  • Congress
  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Clinical Trials as Topic
  • DNA Damage
  • Fanconi Anemia / physiopathology
  • Fanconi Anemia / therapy*
  • Fanconi Anemia Complementation Group A Protein / genetics*
  • Genetic Therapy / adverse effects
  • Genetic Therapy / methods*
  • Genetic Therapy / trends
  • Humans

Substances

  • FANCA protein, human
  • Fanconi Anemia Complementation Group A Protein