Abstract
By exome sequencing, we found de novo SMARCB1 mutations in two of five individuals with typical Coffin-Siris syndrome (CSS), a rare autosomal dominant anomaly syndrome. As SMARCB1 encodes a subunit of the SWItch/Sucrose NonFermenting (SWI/SNF) complex, we screened 15 other genes encoding subunits of this complex in 23 individuals with CSS. Twenty affected individuals (87%) each had a germline mutation in one of six SWI/SNF subunit genes, including SMARCB1, SMARCA4, SMARCA2, SMARCE1, ARID1A and ARID1B.
Publication types
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Research Support, Non-U.S. Gov't
MeSH terms
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Abnormalities, Multiple / genetics*
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Cells, Cultured
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Chromosomal Proteins, Non-Histone / genetics
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DNA Copy Number Variations / genetics
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DNA Helicases / genetics
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DNA-Binding Proteins / genetics
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Exome
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Face / abnormalities
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Female
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Hand Deformities, Congenital / genetics*
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Humans
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Intellectual Disability / genetics*
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Male
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Micrognathism / genetics*
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Mutation, Missense
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Neck / abnormalities
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Nuclear Proteins / genetics
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SMARCB1 Protein
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Sequence Analysis, DNA
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Transcription Factors / genetics
Substances
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ARID1A protein, human
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ARID1B protein, human
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Chromosomal Proteins, Non-Histone
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DNA-Binding Proteins
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Nuclear Proteins
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SMARCA2 protein, human
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SMARCB1 Protein
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SMARCB1 protein, human
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SMARCE1 protein, human
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Transcription Factors
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SMARCA4 protein, human
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DNA Helicases