Reprogramming based gene therapy for inherited red blood cell disorders

Cell Res. 2012 Jun;22(6):941-4. doi: 10.1038/cr.2012.54. Epub 2012 Apr 3.
No abstract available

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Anemia, Sickle Cell / genetics
  • Anemia, Sickle Cell / pathology
  • Cellular Reprogramming*
  • Genetic Therapy*
  • Hematologic Diseases / genetics
  • Hematologic Diseases / therapy*
  • Hematopoietic Stem Cell Transplantation
  • Humans
  • Induced Pluripotent Stem Cells / cytology
  • Induced Pluripotent Stem Cells / metabolism
  • Thalassemia / genetics
  • Thalassemia / metabolism
  • Thalassemia / pathology
  • beta-Globins / genetics
  • beta-Globins / metabolism

Substances

  • beta-Globins