[Three patients with primary AL amyloidosis treated by high-dose melphalan with autologous peripheral blood stem cell transplantation]

Gan To Kagaku Ryoho. 2012 Apr;39(4):625-7.
[Article in Japanese]

Abstract

We present three long-term survivors treated with high-dose melphalan with autologous peripheral blood stem cell transplantation(auto PBSCT)for primary AL amyloidosis. Because melphalan toxicity is dose-related, patient age and the extent of organ involvement are very important factors for the success of high-dose melphalan treatment with PBSCT. The patients were therefore given high-dose melphalan using the risk-adapted approach to melphalan dosing. They received 3 courses of a vincristine, doxorubicin and dexamethasone(VAD)regimen, along with high-dose melphalan(100-200mg/m2)with auto PBSCT. There were no serious complications or transplantation-related mortalities. Patients survived for an average of 68 months(22-100 months)in partial response. A risk-adapted approach to melphalan dosing with PBSCT is an effective treatment in patients with primary AL amyloidosis.

Publication types

  • Case Reports

MeSH terms

  • Amyloidosis / drug therapy*
  • Amyloidosis / pathology
  • Amyloidosis / surgery
  • Biopsy
  • Combined Modality Therapy
  • Female
  • Humans
  • Immunoglobulin Light-chain Amyloidosis
  • Male
  • Melphalan / administration & dosage
  • Melphalan / therapeutic use*
  • Middle Aged
  • Peripheral Blood Stem Cell Transplantation*

Substances

  • Melphalan