A missense mutation in the extracellular domain of Fas: the most common change in Argentinean patients with autoimmune lymphoproliferative syndrome represents a founder effect

J Clin Immunol. 2012 Dec;32(6):1197-203. doi: 10.1007/s10875-012-9731-y. Epub 2012 Jul 3.

Abstract

Mutations in the Fas gene (TNFRSF6) are the most common causes of Autoimmune Lymphoproliferative Syndrome (ALPS-FAS).

Purpose: In Argentina almost a third of patients with ALPS-FAS present a missense mutation affecting the extracellular cysteine rich domain 2 of Fas, p.Cys107Tyr (C107Y). This change was found in homozygous state in 2 patients from a consanguineous family, and heterozygously, in 3 other patients from 3 unrelated families. In these families, 12 relatives were identified as healthy carriers of the mutation. We sought to test the hypothesis that this mutation actually represents a single haplotype of TNFRSF6.

Methods: DNAs from ALPS-C107Y patients and their families, as well as from 150 Argentinean control subjects were sequenced for the known higher frequency single nucleotide polymorphisms (SNPs) of TNFRSF6. The C107Y-carriers were also genotyped at 5 microsatellites proximal to the Fas gene locus.

Results: All C107Y alleles presented a unique intragenic haplotype that could be restricted to this group. Extent of haplotype sharing and variability of microsatellite alleles in C107Y chromosomes support the presence of a single haplotype block including the mutation and encompassing 2.395 Mb.

Conclusions: A founder effect for C107Y has been evidenced in this work and the most common recent ancestor to the patients probably lived 350 years ago. This constitutes the first report of a founder event in ALPS.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Adult
  • Alleles
  • Argentina
  • Autoimmune Lymphoproliferative Syndrome / genetics*
  • Autoimmune Lymphoproliferative Syndrome / pathology
  • Base Sequence
  • Case-Control Studies
  • Child
  • Female
  • Founder Effect*
  • Haplotypes
  • Heterozygote
  • Homozygote
  • Humans
  • Male
  • Microsatellite Repeats
  • Molecular Sequence Data
  • Mutation, Missense*
  • Pedigree
  • Polymorphism, Single Nucleotide*
  • Protein Structure, Tertiary
  • Sequence Analysis, DNA
  • fas Receptor / genetics*

Substances

  • FAS protein, human
  • fas Receptor