Nonviral-mediated hepatic expression of IGF-I increases Treg levels and suppresses autoimmune diabetes in mice

Diabetes. 2013 Feb;62(2):551-60. doi: 10.2337/db11-1776. Epub 2012 Oct 25.

Abstract

In type 1 diabetes, loss of tolerance to β-cell antigens results in T-cell-dependent autoimmune destruction of β cells. The abrogation of autoreactive T-cell responses is a prerequisite to achieve long-lasting correction of the disease. The liver has unique immunomodulatory properties and hepatic gene transfer results in tolerance induction and suppression of autoimmune diseases, in part by regulatory T-cell (Treg) activation. Hence, the liver could be manipulated to treat or prevent diabetes onset through expression of key genes. IGF-I may be an immunomodulatory candidate because it prevents autoimmune diabetes when expressed in β cells or subcutaneously injected. Here, we demonstrate that transient, plasmid-derived IGF-I expression in mouse liver suppressed autoimmune diabetes progression. Suppression was associated with decreased islet inflammation and β-cell apoptosis, increased β-cell replication, and normalized β-cell mass. Permanent protection depended on exogenous IGF-I expression in liver nonparenchymal cells and was associated with increased percentage of intrapancreatic Tregs. Importantly, Treg depletion completely abolished IGF-I-mediated protection confirming the therapeutic potential of these cells in autoimmune diabetes. This study demonstrates that a nonviral gene therapy combining the immunological properties of the liver and IGF-I could be beneficial in the treatment of the disease.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Apoptosis / genetics
  • Apoptosis / immunology
  • Cell Division / genetics
  • Cell Division / immunology
  • Diabetes Mellitus, Experimental / therapy*
  • Diabetes Mellitus, Type 1 / therapy*
  • Genetic Therapy*
  • Humans
  • Insulin-Like Growth Factor I / genetics*
  • Insulin-Secreting Cells / immunology
  • Insulin-Secreting Cells / pathology
  • Liver / immunology
  • Liver / metabolism*
  • Mice
  • Mice, Transgenic
  • Pancreatitis / genetics
  • Pancreatitis / immunology
  • Plasmids / genetics
  • T-Lymphocytes, Regulatory / immunology*

Substances

  • Insulin-Like Growth Factor I