Clinical and immunologic responses in melanoma patients vaccinated with MAGE-A3-genetically modified lymphocytes

Int J Cancer. 2013 Jun 1;132(11):2557-66. doi: 10.1002/ijc.27939. Epub 2012 Dec 13.

Abstract

Cancer vaccines have recently been shown to induce some clinical benefits. The relationship between clinical activity and anti-vaccine T cell responses is somewhat controversial. Indeed, in many trials it has been documented that the induction of vaccine-specific T cells exceeds the clinical responses observed. Here, we evaluate immunological and clinical responses in 23 MAGE-A3(+) melanoma patients treated with autologous lymphocytes genetically engineered to express the tumor antigen MAGE-A3 and the viral gene product thymidine kinase of the herpes simplex virus (HSV-TK). HSV-TK was used as safety system in case of adverse events and as tracer antigen to monitor the immune competence of treated patients. The increase of anti-TK and anti-MAGE-A3 T-cells after vaccination was observed in 90 and 27% of patients, respectively. Among 19 patients with measurable disease, we observed a disease control rate of 26.3%, with one objective clinical response, and four durable, stable diseases. Three patients out of five with no evidence of disease (NED) at the time of vaccination remained NED after 73+, 70+ and 50+ months. Notably, we report that only patients experiencing MAGE-A3-specific immune responses showed a clinical benefit. Additionally, we report that responder and non-responder patients activate and expand T cells against the tracer antigen TK in a similar way, suggesting that local rather than systemic immune suppression might be involved in limiting clinically relevant antitumor immune responses.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Aged
  • Antigens, Neoplasm / immunology*
  • Bone Neoplasms / immunology
  • Bone Neoplasms / mortality
  • Bone Neoplasms / therapy
  • Cancer Vaccines / therapeutic use*
  • Clinical Trials, Phase II as Topic
  • Female
  • Follow-Up Studies
  • Genetic Therapy*
  • Humans
  • Hypersensitivity, Delayed
  • Liver Neoplasms / immunology
  • Liver Neoplasms / mortality
  • Liver Neoplasms / therapy
  • Lung Neoplasms / immunology
  • Lung Neoplasms / mortality
  • Lung Neoplasms / therapy
  • Male
  • Melanoma / immunology*
  • Melanoma / mortality
  • Melanoma / therapy
  • Middle Aged
  • Neoplasm Proteins / immunology*
  • Neoplasm Staging
  • Skin Neoplasms / immunology
  • Skin Neoplasms / mortality
  • Skin Neoplasms / therapy
  • T-Lymphocytes / immunology*
  • T-Lymphocytes / metabolism
  • Thymidine Kinase / immunology
  • Thymidine Kinase / metabolism

Substances

  • Antigens, Neoplasm
  • Cancer Vaccines
  • MAGEA3 protein, human
  • Neoplasm Proteins
  • Thymidine Kinase