Hereditary causes of kidney stones and chronic kidney disease

Pediatr Nephrol. 2013 Oct;28(10):1923-42. doi: 10.1007/s00467-012-2329-z. Epub 2013 Jan 20.

Abstract

Adenine phosphoribosyltransferase (APRT) deficiency, cystinuria, Dent disease, familial hypomagnesemia with hypercalciuria and nephrocalcinosis (FHHNC), and primary hyperoxaluria (PH) are rare but important causes of severe kidney stone disease and/or chronic kidney disease in children. Recurrent kidney stone disease and nephrocalcinosis, particularly in pre-pubertal children, should alert the physician to the possibility of an inborn error of metabolism as the underlying cause. Unfortunately, the lack of recognition and knowledge of the five disorders has frequently resulted in an unacceptable delay in diagnosis and treatment, sometimes with grave consequences. A high index of suspicion coupled with early diagnosis may reduce or even prevent the serious long-term complications of these diseases. In this paper, we review the epidemiology, clinical features, diagnosis, treatment, and outcome of patients with APRT deficiency, cystinuria, Dent disease, FHHNC, and PH, with an emphasis on childhood manifestations.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't
  • Review

MeSH terms

  • Adenine Phosphoribosyltransferase / deficiency*
  • Adenine Phosphoribosyltransferase / genetics
  • Animals
  • Child
  • Cystinuria / diagnosis
  • Cystinuria / epidemiology
  • Cystinuria / genetics*
  • Cystinuria / therapy
  • Dent Disease / diagnosis
  • Dent Disease / epidemiology
  • Dent Disease / genetics*
  • Dent Disease / therapy
  • Genetic Predisposition to Disease
  • Heredity
  • Humans
  • Hypercalciuria / diagnosis
  • Hypercalciuria / epidemiology
  • Hypercalciuria / genetics*
  • Hypercalciuria / therapy
  • Hyperoxaluria, Primary / diagnosis
  • Hyperoxaluria, Primary / epidemiology
  • Hyperoxaluria, Primary / genetics*
  • Hyperoxaluria, Primary / therapy
  • Kidney Calculi / diagnosis
  • Kidney Calculi / epidemiology
  • Kidney Calculi / genetics*
  • Kidney Calculi / therapy
  • Metabolism, Inborn Errors / diagnosis
  • Metabolism, Inborn Errors / epidemiology
  • Metabolism, Inborn Errors / genetics*
  • Metabolism, Inborn Errors / therapy
  • Nephrocalcinosis / diagnosis
  • Nephrocalcinosis / epidemiology
  • Nephrocalcinosis / genetics*
  • Nephrocalcinosis / therapy
  • Phenotype
  • Prognosis
  • Renal Insufficiency, Chronic / diagnosis
  • Renal Insufficiency, Chronic / epidemiology
  • Renal Insufficiency, Chronic / genetics*
  • Renal Insufficiency, Chronic / therapy
  • Renal Tubular Transport, Inborn Errors / diagnosis
  • Renal Tubular Transport, Inborn Errors / epidemiology
  • Renal Tubular Transport, Inborn Errors / genetics*
  • Renal Tubular Transport, Inborn Errors / therapy
  • Risk Factors
  • Urolithiasis / diagnosis
  • Urolithiasis / epidemiology
  • Urolithiasis / genetics*
  • Urolithiasis / therapy

Substances

  • Adenine Phosphoribosyltransferase

Supplementary concepts

  • Adenine phosphoribosyltransferase deficiency
  • Hypomagnesemia primary