Molecular assessment of minimal residual disease in PBSC harvests provides prognostic information in neuroblastoma

Pediatr Blood Cancer. 2013 Sep;60(9):E109-12. doi: 10.1002/pbc.24538. Epub 2013 Mar 21.

Abstract

As almost all patients with high-risk neuroblastomas have autograft, we aimed to determine if minimal residual disease (MRD) quantified by RT-PCR for tyrosine hydroxylase in PBSC is prognostic in neuroblastomas. PBSC harvests from 38 children were analyzed. Seven had harvests positive for TH-mRNA. Patients with a positive MRD had a lower 2-year-overall-survival compared to those with negative MRD (P = 0.04) regardless of whether or not PBSC were re-infused. Patients in CR/VGPR group with positive MRD have hazard ratio of death at 7.3 [1.3-40.5]. In conclusion, molecular MRD status in PBSC of good response group may be of interest as a survival prognostic factor in high-risk neuroblastomas.

Keywords: RQ-PCR for tyrosine hydroxylase mRNA; minimal residual disease; neuroblastoma; peripheral blood stem cells.

Publication types

  • Clinical Trial
  • Multicenter Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Child
  • Child, Preschool
  • Disease-Free Survival
  • Female
  • Humans
  • Infant
  • Male
  • Neoplasm Proteins / genetics
  • Neoplasm Proteins / metabolism
  • Neoplasm, Residual
  • Neuroblastoma / enzymology
  • Neuroblastoma / genetics
  • Neuroblastoma / mortality*
  • Neuroblastoma / therapy*
  • Peripheral Blood Stem Cell Transplantation*
  • Prospective Studies
  • RNA, Messenger / genetics
  • RNA, Messenger / metabolism
  • RNA, Neoplasm / genetics
  • RNA, Neoplasm / metabolism
  • Survival Rate
  • Transplantation, Autologous
  • Tyrosine 3-Monooxygenase / genetics
  • Tyrosine 3-Monooxygenase / metabolism

Substances

  • Neoplasm Proteins
  • RNA, Messenger
  • RNA, Neoplasm
  • Tyrosine 3-Monooxygenase