Novel small-molecule inhibitors of Bcl-XL to treat lung cancer

Cancer Res. 2013 Sep 1;73(17):5485-96. doi: 10.1158/0008-5472.CAN-12-2272. Epub 2013 Jul 3.

Abstract

Bcl-XL is a major antiapoptotic protein in the Bcl-2 family whose overexpression is more widely observed in human lung cancer cells than that of Bcl-2, suggesting that Bcl-XL is more biologically relevant and therefore a better therapeutic target for lung cancer. Here, we screened small molecules that selectively target the BH3 domain (aa 90-98) binding pocket of Bcl-XL using the UCSF DOCK 6.1 program suite and the NCI chemical library database. We identified two new Bcl-XL inhibitors (BXI-61 and BXI-72) that exhibit selective toxicity against lung cancer cells compared with normal human bronchial epithelial cells. Fluorescence polarization assay reveals that BXI-61 and BXI-72 preferentially bind to Bcl-XL protein but not Bcl2, Bcl-w, Bfl-1/A1, or Mcl-1 in vitro with high binding affinities. Treatment of cells with BXI-72 results in disruption of Bcl-XL/Bak or Bcl-XL/Bax interaction, oligomerization of Bak, and cytochrome c release from mitochondria. Importantly, BXI-61 and BXI-72 exhibit more potent efficacy against human lung cancer than ABT-737 but less degree in platelet reduction in vivo. BXI-72 overcomes acquired radioresistance of lung cancer. On the basis of our findings, the development of BXI(s) as a new class of anticancer agents is warranted and represents a novel strategy for improving lung cancer outcome.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Acridines / pharmacology*
  • Aminopyridines / pharmacology*
  • Animals
  • Apoptosis / drug effects
  • Apoptosis / radiation effects
  • Benzimidazoles / pharmacology*
  • Biphenyl Compounds / pharmacology*
  • Blotting, Western
  • Cell Proliferation / drug effects
  • Cell Proliferation / radiation effects
  • Cytochromes c / metabolism
  • Female
  • Humans
  • Lung / cytology
  • Lung / drug effects*
  • Lung Neoplasms / drug therapy*
  • Lung Neoplasms / mortality
  • Lung Neoplasms / pathology
  • Mice
  • Mice, Nude
  • Nitrophenols / pharmacology*
  • Piperazines / pharmacology
  • Protein Multimerization
  • Proto-Oncogene Proteins c-bcl-2 / antagonists & inhibitors*
  • Proto-Oncogene Proteins c-bcl-2 / metabolism
  • Radiation Tolerance / drug effects*
  • Radiation, Ionizing
  • Small Molecule Libraries*
  • Sulfonamides / pharmacology*
  • Survival Rate
  • bcl-2 Homologous Antagonist-Killer Protein / antagonists & inhibitors
  • bcl-2 Homologous Antagonist-Killer Protein / metabolism
  • bcl-X Protein / antagonists & inhibitors*
  • bcl-X Protein / metabolism

Substances

  • ABT-737
  • Acridines
  • Aminopyridines
  • BAK1 protein, human
  • BXI-61
  • BXI-72
  • Benzimidazoles
  • Biphenyl Compounds
  • Nitrophenols
  • Piperazines
  • Proto-Oncogene Proteins c-bcl-2
  • Small Molecule Libraries
  • Sulfonamides
  • bcl-2 Homologous Antagonist-Killer Protein
  • bcl-X Protein
  • Cytochromes c