ZEB2, a new candidate gene for asplenia

Orphanet J Rare Dis. 2014 Jan 8:9:2. doi: 10.1186/1750-1172-9-2.

Abstract

Primary asplenia is a rare condition with poorly known etiology. Mowat-Wilson syndrome (MWS) is characterized by typical facial dysmorphisms, intellectual disability, microcephaly, epilepsy and the possible presence of internal organ malformations. It is caused by heterozygous mutations or deletions in the ZEB2 gene. Nearly 180 patients have been reported to date, but only one with asplenia. We report here spleen hypo/aplasia in 4 out of 6 MWS patients, with severe infectious complications for 3 of them. Our report shows that spleen hypo/aplasia is part of the MWS phenotype and makes ZEB2 a possible candidate gene for primary asplenia.

Publication types

  • Case Reports
  • Letter

MeSH terms

  • Facies
  • Female
  • Heterotaxy Syndrome / genetics*
  • Hirschsprung Disease / genetics*
  • Homeodomain Proteins / genetics*
  • Humans
  • Intellectual Disability / genetics*
  • Microcephaly / genetics*
  • Repressor Proteins / genetics*
  • Zinc Finger E-box Binding Homeobox 2

Substances

  • Homeodomain Proteins
  • Repressor Proteins
  • ZEB2 protein, human
  • Zinc Finger E-box Binding Homeobox 2

Supplementary concepts

  • Mowat-Wilson syndrome