Leukoencephalopathy with brain stem and spinal cord involvement and lactate elevation: high outcome variation between two siblings

Neuropediatrics. 2014 Jun;45(3):188-91. doi: 10.1055/s-0033-1364105. Epub 2014 Jan 9.

Abstract

Leukoencephalopathy with brain stem and spinal cord involvement and lactate elevation is a rare disorder caused by mutations in the gene encoding a mitochondrial aspartyl-tRNA synthetase, DARS2. Clinical features include childhood or adolescent onset, slowly progressive ataxia, spasticity, and dorsal column dysfunction with or without mild cognitive decline. Magnetic resonance (MR) images show a characteristic leukoencephalopathy with multiple long tract involvement. MR spectroscopy shows elevated levels of lactate. We present strikingly different clinical courses and discrepant MR images findings for a pair of brothers. It cannot be excluded that in the cases presented, the different clinical outcome is related to a varicella infection in infancy in the younger brother.

Publication types

  • Case Reports

MeSH terms

  • Adult
  • Brain / pathology*
  • Diffusion Magnetic Resonance Imaging
  • Humans
  • Lactic Acid / metabolism*
  • Leukoencephalopathies / metabolism*
  • Leukoencephalopathies / pathology*
  • Magnetic Resonance Imaging
  • Male
  • Siblings
  • Spinal Cord / pathology*

Substances

  • Lactic Acid