A new era in the treatment of cystic fibrosis

Clin Med (Lond). 2014 Feb;14(1):76-8. doi: 10.7861/clinmedicine.14-1-76.
No abstract available

Keywords: Ataluren; cystic fibrosis; gene therapy; ivacaftor; lumacaftor ▪.

MeSH terms

  • Aminophenols / therapeutic use
  • Aminopyridines / therapeutic use
  • Benzodioxoles / therapeutic use
  • Cystic Fibrosis / genetics*
  • Cystic Fibrosis / therapy*
  • Cystic Fibrosis Transmembrane Conductance Regulator / genetics*
  • Genetic Therapy
  • Humans
  • Molecular Targeted Therapy
  • Mutation*
  • Oxadiazoles / therapeutic use
  • Quinolones / therapeutic use

Substances

  • Aminophenols
  • Aminopyridines
  • Benzodioxoles
  • CFTR protein, human
  • Oxadiazoles
  • Quinolones
  • Cystic Fibrosis Transmembrane Conductance Regulator
  • ivacaftor
  • lumacaftor
  • ataluren