CALR exon 9 mutations are somatically acquired events in familial cases of essential thrombocythemia or primary myelofibrosis

Blood. 2014 Apr 10;123(15):2416-9. doi: 10.1182/blood-2014-01-550434. Epub 2014 Feb 19.

Abstract

Somatic mutations in the calreticulin (CALR) gene were recently discovered in patients with sporadic essential thrombocythemia (ET) and primary myelofibrosis (PMF) lacking JAK2 and MPL mutations. We studied CALR mutation status in familial cases of myeloproliferative neoplasm. In a cohort of 127 patients, CALR indels were identified in 6 of 55 (11%) subjects with ET and in 6 of 20 (30%) with PMF, whereas 52 cases of polycythemia vera had nonmutated CALR. All CALR mutations were somatic, found in granulocytes but not in T lymphocytes. Patients with CALR-mutated ET showed a higher platelet count (P = .017) and a lower cumulative incidence of thrombosis (P = .036) and of disease progression (P = .047) compared with those with JAK2 (V617F). In conclusion, a significant proportion of familial ET and PMF nonmutated for JAK2 carry a somatic mutation of CALR.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Calreticulin / genetics*
  • DNA Mutational Analysis
  • Exons / genetics
  • Genetic Predisposition to Disease
  • Genotype
  • Humans
  • Janus Kinase 2 / genetics
  • Kaplan-Meier Estimate
  • Mutation*
  • Pedigree
  • Phenotype
  • Primary Myelofibrosis / genetics*
  • Primary Myelofibrosis / mortality
  • Thrombocythemia, Essential / genetics*
  • Thrombocythemia, Essential / mortality

Substances

  • CALR protein, human
  • Calreticulin
  • JAK2 protein, human
  • Janus Kinase 2