Allo-SCT for Philadelphia-negative myeloproliferative neoplasms in blast phase: a study from the Societe Française de Greffe de Moelle et de Therapie Cellulaire (SFGM-TC)

Bone Marrow Transplant. 2014 Jun;49(6):756-60. doi: 10.1038/bmt.2014.31. Epub 2014 Mar 10.

Abstract

Progression of Philadelphia-negative myeloproliferative (MPN) or myelodysplastic/myeloproliferative neoplasms (MDS/MPN) to acute myeloid leukemia (AML) is an adverse event in the course of the disease. Although allogeneic hematopoietic SCT (allo-SCT) is considered as the only curative therapy, few data exist on the outcome of patients with Philadelphia-negative MPN or MDS/MPN in blast phase who received an allo-SCT. Sixty patients were included in this retrospective study. AML was secondary to an MPN in 43 cases, whereas AML evolved from an MDS/MPN in 17 cases. Patients received allo-SCT in CR or advanced disease in 26 cases and 34 cases, respectively. With a median follow-up of 31 months (range, 25-44), OS and leukemia-free survival (LFS) were, respectively, 18% and 9% at 3 years. CR at transplant was associated with an improved LFS in univariate and multivariate analysis. The 3-year LFS was 18% for patients undergoing allo-SCT in CR versus 3% in advanced disease (P=0.008). Absence of thrombosis and an intermediate or favorable AML karyotype were associated with an improved outcome for patients who received allo-SCT in CR. New strategies are needed to improve the outcome of patients with MPN-MDS/MPN in blast phase.

Publication types

  • Multicenter Study

MeSH terms

  • Adult
  • Aged
  • Allografts
  • Blast Crisis / therapy*
  • Disease-Free Survival
  • Female
  • France
  • Hematopoietic Stem Cell Transplantation*
  • Humans
  • Kaplan-Meier Estimate
  • Leukemia, Myeloid, Chronic, Atypical, BCR-ABL Negative / pathology*
  • Leukemia, Myeloid, Chronic, Atypical, BCR-ABL Negative / therapy*
  • Male
  • Middle Aged
  • Myelodysplastic-Myeloproliferative Diseases / pathology*
  • Myelodysplastic-Myeloproliferative Diseases / therapy*
  • Retrospective Studies