Dendronized nanoconjugates of lysine and folate for treatment of cancer

Eur J Pharm Biopharm. 2014 Aug;87(3):500-9. doi: 10.1016/j.ejpb.2014.03.015. Epub 2014 Mar 31.

Abstract

Poly-L-lysine (PLL) dendrimers are currently being investigated as antiangiogenic agent for therapy of cancer. In this study, we report folate conjugated poly-l-lysine dendrimers (FPLL) as an efficient carrier for model anticancer drug, doxorubicin hydrochloride (Dox); for pH sensitive drug release, selective targeting to cancer cells, anticancer activity and antiangiogenic activity. This nanoconjugate of Dox showed initial rapid in vitro release followed by gradual slow release, and the drug release was found to be pH sensitive with greater release at acidic pH. In the CAM assay and tubule formation assay with HUVEC, Dox-FPLL formulation showed the significant antiangiogenic activity confirming that activity of PLL was not compromised by the presence of Dox and folic acid. The ex vivo investigations with human breast cancer cell lines MCF-7 showed enhanced cytotoxicity of Dox-FPLL with significantly enhanced intracellular uptake (p<0.001). The in vivo therapeutic potential of nanoconjugate was determined in MCF-7 breast cancer xenograft model in tumor-bearing mice. Dox-FPLL increased the concentration of Dox in tumor by 121.5-fold after 24 h in comparison with free Dox formulation. The folate conjugated dendrimeric Dox showed superior anti-tumor activity in tumor xenograft model with significantly prolonged survival determined by Kaplan Meier survival analysis (p<0.001).

Keywords: Angiogenesis; Dendrimers; Drug delivery; Folic acid; Lysine; Nanoconjugate.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Angiogenesis Inhibitors / chemistry
  • Angiogenesis Inhibitors / pharmacology
  • Animals
  • Antineoplastic Agents / chemistry*
  • Antineoplastic Agents / pharmacology*
  • Cell Line, Tumor
  • Chemistry, Pharmaceutical / methods
  • Dendrimers / chemistry*
  • Doxorubicin / chemistry
  • Doxorubicin / pharmacology
  • Drug Carriers / chemistry
  • Drug Delivery Systems / methods
  • Folic Acid / chemistry*
  • Humans
  • Hydrogen-Ion Concentration
  • Lysine / chemistry*
  • MCF-7 Cells
  • Mice
  • Mice, Inbred BALB C
  • Nanoconjugates / chemistry*
  • Xenograft Model Antitumor Assays

Substances

  • Angiogenesis Inhibitors
  • Antineoplastic Agents
  • Dendrimers
  • Drug Carriers
  • Nanoconjugates
  • Doxorubicin
  • Folic Acid
  • Lysine