Therapeutic protein aggregation: mechanisms, design, and control

Trends Biotechnol. 2014 Jul;32(7):372-80. doi: 10.1016/j.tibtech.2014.05.005. Epub 2014 Jun 4.

Abstract

Although it is well known that proteins are only marginally stable in their folded states, it is often less well appreciated that most proteins are inherently aggregation-prone in their unfolded or partially unfolded states, and the resulting aggregates can be extremely stable and long-lived. For therapeutic proteins, aggregates are a significant risk factor for deleterious immune responses in patients, and can form via a variety of mechanisms. Controlling aggregation using a mechanistic approach may allow improved design of therapeutic protein stability, as a complement to existing design strategies that target desired protein structures and function. Recent results highlight the importance of balancing protein environment with the inherent aggregation propensities of polypeptide chains.

Keywords: computational design; protein aggregation; protein interactions; protein stability.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, U.S. Gov't, Non-P.H.S.
  • Review

MeSH terms

  • Biopharmaceutics
  • Biotechnology
  • Humans
  • Models, Molecular
  • Protein Aggregates
  • Protein Conformation
  • Protein Folding
  • Protein Stability
  • Proteins / chemistry*
  • Proteins / pharmacology*

Substances

  • Protein Aggregates
  • Proteins