Acquired von Willebrand syndrome: von Willebrand factor propeptide to von Willebrand factor antigen ratio predicts remission status

Blood. 2014 Jul 31;124(5):e1-3. doi: 10.1182/blood-2014-02-557132. Epub 2014 Jun 20.

Abstract

We investigated a case of acquired von Willebrand syndrome (AVWS) secondary to a nonneutralizing anti-von Willebrand factor (VWF) antibody associated with an autoimmune disorder. At diagnosis, VWF activity (VWF:Act), antigen (VWF:Ag), multimers, and factor VIII coagulant activity were virtually absent. VWF propeptide (VWFpp) was elevated with an infinitely high VWFpp to VWF:Ag ratio (VWFpp:Ag) consistent with rapid VWF clearance. Immunosuppressive treatment resulted in phenotypic remission 1 with normalization of VWF/factor VIII levels and multimer pattern. However, VWFpp:Ag remained elevated (∼2× normal), consistent with ongoing VWF clearance by the remaining anti-VWF antibody still present by enzyme-linked immunosorbent assay. This suggests that increased VWF secretion was compensating for the incomplete remission state. Relapse occurred when VWFpp:Ag was again infinitely high, with associated decreased VWFpp but unchanged anti-VWF titers; switching the balance to favor VWF clearance over secretion. Complete remission with undetectable anti-VWF occurred only when VWFpp:Ag was normal. This case of relapsing-remitting AVWS demonstrates the use of VWFpp:Ag for predicting remission status.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Autoantibodies / blood*
  • Autoantibodies / immunology
  • Blood Coagulation Disorders / blood*
  • Blood Coagulation Disorders / diagnosis
  • Blood Coagulation Disorders / immunology
  • Blood Coagulation Disorders / therapy
  • Enzyme-Linked Immunosorbent Assay
  • Female
  • Humans
  • Protein Precursors / blood*
  • Protein Precursors / immunology
  • Remission Induction
  • von Willebrand Factor / immunology
  • von Willebrand Factor / metabolism*

Substances

  • Autoantibodies
  • Protein Precursors
  • Von Willebrand antigen
  • von Willebrand Factor
  • von Willebrand factor propolypeptide