A novel BET bromodomain inhibitor, RVX-208, shows reduction of atherosclerosis in hyperlipidemic ApoE deficient mice

Atherosclerosis. 2014 Sep;236(1):91-100. doi: 10.1016/j.atherosclerosis.2014.06.008. Epub 2014 Jun 28.

Abstract

Despite the benefit of statins in reducing cardiovascular risk, a sizable proportion of patients still remain at risk. Since HDL reduces CVD risk through a process that involves formation of pre-beta particles that facilitates the removal of cholesterol from the lipid-laden macrophages in the arteries, inducing pre-beta particles, may reduce the risk of CVD. A novel BET bromodomain antagonist, RVX-208, was reported to raise apoA-I and increase preβ-HDL particles in non-human primates and humans. In the present study, we investigated the effect of RVX-208 on aortic lesion formation in hyperlipidemic apoE(-/-) mice. Oral treatments of apoE(-/-) mice with 150 mg/kg b.i.d RVX-208 for 12 weeks significantly reduced aortic lesion formation, accompanied by 2-fold increases in the levels of circulating HDL-C, and ∼50% decreases in LDL-C, although no significant changes in plasma apoA-I were observed. Circulating adhesion molecules as well as cytokines also showed significant reduction. Haptoglobin, a proinflammatory protein, known to bind with HDL/apoA-I, decreased >2.5-fold in the RVX-208 treated group. With a therapeutic dosing regimen in which mice were fed Western diet for 10 weeks to develop lesions followed by switching to a low fat diet and concurrent treatment with RVX-208 for 14 weeks, RVX-208 similarly reduced lesion formation by 39% in the whole aorta without significant changes in the plasma lipid parameters. RVX-208 significantly reduced the proinflammatory cytokines IP-10, MIP1(®) and MDC. These results show that the antiatherogenic activity of BET inhibitor, RVX-208, occurs via a combination of lipid changes and anti-inflammatory activities.

Keywords: Atherosclerosis; BET inhibitor; Inflammation; Preβ-HDL; RVX-208; apoA-I-inducer; apoE deficient.

MeSH terms

  • Animals
  • Aorta / drug effects
  • Aorta / metabolism
  • Aorta / pathology
  • Aortic Diseases / blood
  • Aortic Diseases / etiology
  • Aortic Diseases / pathology
  • Aortic Diseases / prevention & control*
  • Apolipoprotein A-I / blood
  • Apolipoproteins E / deficiency
  • Atherosclerosis / blood
  • Atherosclerosis / etiology
  • Atherosclerosis / pathology
  • Atherosclerosis / prevention & control*
  • Betaine-Homocysteine S-Methyltransferase / antagonists & inhibitors*
  • Cell Line
  • Cholesterol, HDL / blood
  • Cholesterol, LDL / blood
  • Cytokines / blood
  • Diet, Fat-Restricted
  • Diet, Western / adverse effects
  • Drug Evaluation, Preclinical
  • Endothelial Cells
  • Gene Expression Profiling
  • Humans
  • Hyperlipidemias / blood
  • Hyperlipidemias / complications
  • Hyperlipidemias / diet therapy
  • Hyperlipidemias / drug therapy*
  • Hyperlipidemias / genetics
  • Inflammation / blood
  • Inflammation / prevention & control
  • Liver / drug effects
  • Liver / metabolism
  • Male
  • Mice
  • Mice, Inbred C57BL
  • Mice, Knockout
  • Quinazolines / pharmacology
  • Quinazolines / therapeutic use*
  • Quinazolinones
  • RNA, Messenger / analysis
  • U937 Cells

Substances

  • Apolipoprotein A-I
  • Apolipoproteins E
  • Cholesterol, HDL
  • Cholesterol, LDL
  • Cytokines
  • Quinazolines
  • Quinazolinones
  • RNA, Messenger
  • apabetalone
  • Betaine-Homocysteine S-Methyltransferase