Three cost-utility analyses of screening for intracranial hemorrhage in neonates with hemophilia

J Pediatr Hematol Oncol. 2014 Aug;36(6):474-9. doi: 10.1097/MPH.0000000000000174.

Abstract

Background: Intracranial hemorrhage (ICH) in the newborn period is a potential cause of serious morbidity and mortality in individuals with hemophilia. The incidence of ICH is estimated to be 2% to 4%; however, depending on the mode of delivery, it may be considerably higher. Considering the varying sensitivities and costs of various imaging modalities, there remains controversy surrounding universal cranial imaging. Cost-utility analysis is the ideal tool to display the consequences of a decision made.

Methods: We constructed a decision tree to evaluate the direct and indirect costs, possible outcomes, and probabilities of ICH in neonates with hemophilia. We created 3 decision analysis models to evaluate the cost-utility of different screening modalities for ICH: ultrasound, computed tomography, and magnetic resonance imaging. Within each model, 3 different strategies were compared: screen all neonates; screen only neonates born by instrumented delivery; and not screen any neonates. A societal perspective was used for all models. The base case models were later reanalyzed in sensitivity analysis to account for uncertainties.

Results: Total costs for screening all neonates, screening only neonates born by instrumented delivery, and not screening any neonates were $9501, $9297, and $9347, respectively, for US, and $9761, $9351, and $9353, respectively, for CT. Screening instrumented deliveries using MRI had an incremental cost-effectiveness ratio of $12,440.

Conclusions: Screening newborns born by an instrumented delivery appears to be the most cost-effective strategy irrespective of the imaging modality. Subsequent studies will require a longer time frame to factor in possible late effects of radiation, anesthesia, and the high cost of factor replacement and hospital admission.

MeSH terms

  • Cost-Benefit Analysis
  • Decision Support Techniques
  • Decision Trees
  • Health Expenditures
  • Hemophilia A / diagnosis*
  • Hemophilia A / economics*
  • Hemophilia A / epidemiology
  • Humans
  • Infant, Newborn
  • Intracranial Hemorrhages / diagnosis*
  • Intracranial Hemorrhages / economics*
  • Intracranial Hemorrhages / epidemiology
  • Magnetic Resonance Imaging / economics
  • Magnetic Resonance Imaging / statistics & numerical data
  • Neonatal Screening / economics*
  • Neonatal Screening / statistics & numerical data*
  • Prevalence
  • Quality of Life
  • Sensitivity and Specificity
  • Tomography, X-Ray Computed / economics
  • Tomography, X-Ray Computed / statistics & numerical data
  • Ultrasonography / economics
  • Ultrasonography / statistics & numerical data
  • Uncertainty