Clinical and genetic features of acute encephalopathy in children taking theophylline

Brain Dev. 2015 May;37(5):463-70. doi: 10.1016/j.braindev.2014.07.010. Epub 2014 Aug 23.

Abstract

Background: Theophylline has recently been suspected as a risk factor of acute encephalopathy with biphasic seizures and late reduced diffusion (AESD), although there has been no systematic study on the relationship between acute encephalopathy in children taking theophylline (AET) and AESD.

Methods: We recruited 16 Japanese patients (11 male and 5 female, median age of 2 years and 7 months) with AET from 2008 to 2013. We evaluated their clinical features, such as the duration of first seizure, biphasic clinical course and cranial CT/MRI imaging and compared them with those of AESD. We analyzed the polymorphisms or mutations of genes which are associated with AESD.

Results: Clinically, 12 patients had neurological and/or radiological features of AESD. Only one patient died, whereas all 15 surviving patients were left with motor and/or intellectual deficits. Genetically, 14 patients had at least one of the following polymorphisms or mutations associated with AESD: thermolabile variation of the carnitine palmitoyltransferase 2 (CPT2) gene, polymorphism causing high expression of the adenosine receptor A2A (ADORA2A) gene, and heterozygous missense mutation of the voltage gated sodium channel 1A (SCN1A) and 2A (SCN2A) gene.

Conclusions: Our results demonstrate that AET overlaps with AESD, and that AET is a multifactorial disorder sharing a genetic background with AESD.

Keywords: Acute encephalopathy; Adenosine receptors; Status epilepticus; Theophylline.

Publication types

  • Multicenter Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Acute Disease
  • Anti-Asthmatic Agents / administration & dosage*
  • Anti-Asthmatic Agents / adverse effects
  • Brain Diseases / chemically induced
  • Brain Diseases / genetics*
  • Brain Diseases / pathology*
  • Case-Control Studies
  • Child, Preschool
  • Female
  • Genetic Predisposition to Disease
  • Humans
  • Infant
  • Magnetic Resonance Imaging
  • Male
  • Mutation, Missense
  • NAV1.1 Voltage-Gated Sodium Channel / genetics
  • NAV1.2 Voltage-Gated Sodium Channel / genetics
  • Receptor, Adenosine A2A / genetics
  • Theophylline / administration & dosage*
  • Theophylline / adverse effects
  • Tomography, X-Ray Computed

Substances

  • Anti-Asthmatic Agents
  • NAV1.1 Voltage-Gated Sodium Channel
  • NAV1.2 Voltage-Gated Sodium Channel
  • Receptor, Adenosine A2A
  • SCN1A protein, human
  • SCN2A protein, human
  • Theophylline