JNJ-40255293, a novel adenosine A2A/A1 antagonist with efficacy in preclinical models of Parkinson's disease

ACS Chem Neurosci. 2014 Oct 15;5(10):1005-19. doi: 10.1021/cn5001606. Epub 2014 Sep 24.

Abstract

Adenosine A2A antagonists are believed to have therapeutic potential in the treatment of Parkinson's disease (PD). We have characterized the dual adenosine A2A/A1 receptor antagonist JNJ-40255293 (2-amino-8-[2-(4-morpholinyl)ethoxy]-4-phenyl-5H-indeno[1,2-d]pyrimidin-5-one). JNJ-40255293 was a high-affinity (7.5 nM) antagonist at the human A2A receptor with 7-fold in vitro selectivity versus the human A1 receptor. A similar A2A:A1 selectivity was seen in vivo (ED50's of 0.21 and 2.1 mg/kg p.o. for occupancy of rat brain A2A and A1 receptors, respectively). The plasma EC50 for occupancy of rat brain A2A receptors was 13 ng/mL. In sleep-wake encephalographic (EEG) studies, JNJ-40255293 dose-dependently enhanced a consolidated waking associated with a subsequent delayed compensatory sleep (minimum effective dose: 0.63 mg/kg p.o.). As measured by microdialysis, JNJ-40255293 did not affect dopamine and noradrenaline release in the prefrontal cortex and the striatum. However, it was able to reverse effects (catalepsy, hypolocomotion, and conditioned avoidance impairment in rats; hypolocomotion in mice) produced by the dopamine D2 antagonist haloperidol. The compound also potentiated the agitation induced by the dopamine agonist apomorphine. JNJ-40255293 also reversed hypolocomotion produced by the dopamine-depleting agent reserpine and potentiated the effects of l-dihydroxyphenylalanine (L-DOPA) in rats with unilateral 6-hydroxydopamine-induced lesions of the nigro-striatal pathway, an animal model of Parkinson's disease. Extrapolating from the rat receptor occupancy dose-response curve, the occupancy required to produce these various effects in rats was generally in the range of 60-90%. The findings support the continued research and development of A2A antagonists as potential treatments for PD.

Keywords: A2A antagonists; Parkinson’s disease; adenosine; dopamine; neurodegeneration; neuropharmacology.

MeSH terms

  • Adenosine A1 Receptor Antagonists / chemistry
  • Adenosine A1 Receptor Antagonists / pharmacokinetics
  • Adenosine A1 Receptor Antagonists / pharmacology
  • Adenosine A2 Receptor Antagonists / chemistry
  • Adenosine A2 Receptor Antagonists / pharmacokinetics
  • Adenosine A2 Receptor Antagonists / pharmacology
  • Animals
  • Antiparkinson Agents / chemistry
  • Antiparkinson Agents / pharmacokinetics
  • Antiparkinson Agents / pharmacology*
  • Brain / drug effects
  • Brain / physiopathology
  • CHO Cells
  • Cricetulus
  • Dopamine / metabolism
  • Dose-Response Relationship, Drug
  • HEK293 Cells
  • Humans
  • Indenes / chemistry
  • Indenes / pharmacokinetics
  • Indenes / pharmacology*
  • Male
  • Mice
  • Motor Activity / drug effects
  • Norepinephrine / metabolism
  • Parkinsonian Disorders / drug therapy
  • Parkinsonian Disorders / physiopathology
  • Pyrimidines / chemistry
  • Pyrimidines / pharmacokinetics
  • Pyrimidines / pharmacology*
  • Rats, Sprague-Dawley
  • Rats, Wistar
  • Receptor, Adenosine A1 / metabolism
  • Receptor, Adenosine A2A / metabolism
  • Recombinant Proteins / metabolism

Substances

  • 2-amino-8-(2-(4-morpholinyl)ethoxy)-4-phenyl-5H-indeno(1,2-d)pyrimidin-5-one
  • Adenosine A1 Receptor Antagonists
  • Adenosine A2 Receptor Antagonists
  • Antiparkinson Agents
  • Indenes
  • Pyrimidines
  • Receptor, Adenosine A1
  • Receptor, Adenosine A2A
  • Recombinant Proteins
  • Dopamine
  • Norepinephrine