Pharmacoepidemiology of Immune Thrombocytopenia: protocols of FAITH and CARMEN studies

Therapie. 2014 Sep-Oct;69(5):437-48. doi: 10.2515/therapie/2014056. Epub 2014 Oct 7.

Abstract

Immune thrombocytopenia (ITP) is a rare condition. Its epidemiology is not well-known. First-line treatment is based on corticosteroids. ITP leads to persistency (lasting more than 3 months) in 70% of adult cases. Then, several second-line treatments (SLTs) are available, mainly splenectomy, rituximab (off-label) and thrombopoietin-receptor agonists. Their efficacy and safety have not been compared, particularly in the long-term. FAITH (French Adult primary Immune Thrombocytopenia: a pHarmacoepidemiological study) is dedicated to the building and follow-up of the cohort of all adults with primary ITP in France persistently treated (>3 months) through the database of French Health Insurance system (système national d'information interrégimes d'Assurance maladie, SNIIRAM), in order to assess the benefit-to-risk balance of SLTs in real-life practice. CARMEN (Cytopénies Auto-immunes : Registre Midi-PyrénéEN) is a clinical registry of all incident adult ITP patients in the Midi-Pyrénées region. It is aimed at describing ITP clinical features, assessing SLT benefit-to-risk balance and adherence to guidelines for ITP management. FAITH is registered n°ENCEPP/SDPP/4574.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Epidemiologic Research Design
  • France / epidemiology
  • Humans
  • Pharmacoepidemiology / methods
  • Pharmacoepidemiology / statistics & numerical data
  • Purpura, Thrombocytopenic, Idiopathic / drug therapy*
  • Purpura, Thrombocytopenic, Idiopathic / epidemiology*