Total synthesis of 6-deoxypladienolide D and Assessment of Splicing Inhibitory Activity in a Mutant SF3B1 cancer cell line

Org Lett. 2014 Nov 7;16(21):5560-3. doi: 10.1021/ol502556c. Epub 2014 Oct 26.

Abstract

A total synthesis of the natural product 6-deoxypladienolide D (1) has been achieved. Two noteworthy attributes of the synthesis are (1) a late-stage allylic oxidation which proceeds with full chemo-, regio-, and diastereoselectivity and (2) the development of a scalable and cost-effective synthetic route to support drug discovery efforts. 6-Deoxypladienolide D (1) demonstrates potent growth inhibition in a mutant SF3B1 cancer cell line, high binding affinity to the SF3b complex, and inhibition of pre-mRNA splicing.

MeSH terms

  • Antineoplastic Agents / chemical synthesis*
  • Antineoplastic Agents / chemistry
  • Antineoplastic Agents / pharmacology*
  • Binding Sites
  • Cell Line, Tumor / chemistry*
  • Cell Line, Tumor / drug effects*
  • Cell Proliferation / drug effects*
  • Epoxy Compounds / chemical synthesis*
  • Epoxy Compounds / chemistry
  • Epoxy Compounds / metabolism*
  • Humans
  • Macrolides / chemical synthesis*
  • Macrolides / chemistry
  • Macrolides / metabolism*
  • Phosphoproteins / antagonists & inhibitors*
  • Phosphoproteins / chemistry*
  • RNA Splicing / drug effects*
  • RNA Splicing Factors
  • Ribonucleoprotein, U2 Small Nuclear / antagonists & inhibitors*
  • Ribonucleoprotein, U2 Small Nuclear / chemistry*

Substances

  • 6-deoxypladienolide D
  • Antineoplastic Agents
  • Epoxy Compounds
  • Macrolides
  • Phosphoproteins
  • RNA Splicing Factors
  • Ribonucleoprotein, U2 Small Nuclear
  • SF3B1 protein, human