Triazine-modified dendrimer for efficient TRAIL gene therapy in osteosarcoma

Acta Biomater. 2015 Apr:17:115-24. doi: 10.1016/j.actbio.2015.01.007. Epub 2015 Jan 14.

Abstract

Osteosarcoma is a high-grade malignant bone tumor that usually develops in the teenagers. Despite improvement in therapy, the five-year survival rate is poor for patients not responding to treatment or with metastases. Tumor necrosis factor (TNF) related apoptosis inducing ligand (TRAIL) gene therapy is a new strategy in the treatment of cancers, however, the lack of efficient and low toxic vectors remains the major obstacle in TRAIL gene therapy. In this study, a triazine-modified dendrimer G5-DAT66 was synthesized and used as a vector for TRAIL gene therapy in vitro and in vivo. The material shows much higher transfection efficacy on osteosarcoma MG-63 cell line than commercial transfection reagents such as Lipofectamine 2000 and SuperFect. It effectively induces apoptosis in MG-63 cells and three-dimensional MG-63 cell cultures when delivering a TRAIL plasmid. In vivo studies further prove that G5-DAT66 efficiently transfects TRAIL plasmid in tumors and inhibits tumor growth in osteosarcoma-bearing mice. These results suggest that triazine-modified dendrimer has promising potential for TRAIL gene therapy in osteosarcoma.

Keywords: Dendrimer; Gene therapy; Osteosarcoma; TRAIL.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Apoptosis
  • Bone Neoplasms / genetics*
  • Bone Neoplasms / metabolism
  • Bone Neoplasms / therapy
  • Cell Line, Tumor
  • DNA / chemistry
  • Dendrimers / chemistry*
  • Female
  • Genetic Therapy / methods*
  • Genetic Vectors
  • Humans
  • Ligands
  • Mice
  • Mice, Inbred BALB C
  • Neoplasm Transplantation
  • Osteosarcoma / genetics*
  • Osteosarcoma / metabolism
  • Osteosarcoma / therapy
  • Plasmids / metabolism
  • TNF-Related Apoptosis-Inducing Ligand / genetics*
  • Transfection
  • Triazines / chemistry*

Substances

  • Dendrimers
  • Ligands
  • TNF-Related Apoptosis-Inducing Ligand
  • TNFSF10 protein, human
  • Triazines
  • DNA