Pharmaceutical development and preclinical evaluation of a GMP-grade anti-inflammatory nanotherapy

Nanomedicine. 2015 Jul;11(5):1133-40. doi: 10.1016/j.nano.2015.02.020. Epub 2015 Mar 17.

Abstract

The present study describes the development of a good manufacturing practice (GMP)-grade liposomal nanotherapy containing prednisolone phosphate for the treatment of inflammatory diseases. After formulation design, GMP production was commenced which yielded consistent, stable liposomes sized 100nm±10nm, with a prednisolone phosphate (PLP) incorporation efficiency of 3%-5%. Pharmacokinetics and toxicokinetics of GMP-grade liposomal nanoparticles were evaluated in healthy rats, which were compared to daily and weekly administration of free prednisolone phosphate, revealing a long circulatory half-life with minimal side effects. Subsequently, non-invasive multimodal clinical imaging after liposomal nanotherapy's intravenous administration revealed anti-inflammatory effects on the vessel wall of atherosclerotic rabbits. The present program led to institutional review board approval for two clinical trials with patients with atherosclerosis.

From the clinical editor: In drug discovery, bringing production to industrial scale is an essential process. In this article the authors describe the development of an anti-inflammatory nanoparticle according to good manufacturing practice. As a result, this paves the way for translating laboratory studies to clinical trials in humans.

Keywords: Atherosclerosis; Formulation design; GMP-grade; Nanomedicine; Prednisolone phosphate.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Anti-Inflammatory Agents / administration & dosage*
  • Anti-Inflammatory Agents / pharmacokinetics
  • Anti-Inflammatory Agents / therapeutic use
  • Anti-Inflammatory Agents / toxicity
  • Aorta / drug effects
  • Aorta / pathology
  • Atherosclerosis / drug therapy*
  • Atherosclerosis / pathology
  • Chemistry, Pharmaceutical / methods*
  • Glucocorticoids / administration & dosage*
  • Glucocorticoids / pharmacokinetics
  • Glucocorticoids / therapeutic use
  • Glucocorticoids / toxicity
  • Half-Life
  • Humans
  • Liposomes
  • Male
  • Prednisolone / administration & dosage
  • Prednisolone / analogs & derivatives*
  • Prednisolone / pharmacokinetics
  • Prednisolone / therapeutic use
  • Prednisolone / toxicity
  • Rabbits
  • Rats
  • Rats, Sprague-Dawley
  • Rats, Wistar

Substances

  • Anti-Inflammatory Agents
  • Glucocorticoids
  • Liposomes
  • prednisolone phosphate
  • Prednisolone