Novel mutations in TNFRSF7/CD27: Clinical, immunologic, and genetic characterization of human CD27 deficiency

J Allergy Clin Immunol. 2015 Sep;136(3):703-712.e10. doi: 10.1016/j.jaci.2015.02.022. Epub 2015 Apr 3.

Abstract

Background: The clinical and immunologic features of CD27 deficiency remain obscure because only a few patients have been identified to date.

Objective: We sought to identify novel mutations in TNFRSF7/CD27 and to provide an overview of clinical, immunologic, and laboratory phenotypes in patients with CD27 deficiency.

Methods: Review of the medical records and molecular, genetic, and flow cytometric analyses of the patients and family members were performed. Treatment outcomes of previously described patients were followed up.

Results: In addition to the previously reported homozygous mutations c.G24A/p.W8X (n = 2) and c.G158A/p.C53Y (n = 8), 4 novel mutations were identified: homozygous missense c.G287A/p.C96Y (n = 4), homozygous missense c.C232T/p.R78W (n = 1), heterozygous nonsense c.C30A/p.C10X (n = 1), and compound heterozygous c.C319T/p.R107C-c.G24A/p.W8X (n = 1). EBV-associated lymphoproliferative disease/hemophagocytic lymphohistiocytosis, Hodgkin lymphoma, uveitis, and recurrent infections were the predominant clinical features. Expression of cell-surface and soluble CD27 was significantly reduced in patients and heterozygous family members. Immunoglobulin substitution therapy was administered in 5 of the newly diagnosed cases.

Conclusion: CD27 deficiency is potentially fatal and should be excluded in all cases of severe EBV infections to minimize diagnostic delay. Flow cytometric immunophenotyping offers a reliable initial test for CD27 deficiency. Determining the precise role of CD27 in immunity against EBV might provide a framework for new therapeutic concepts.

Keywords: CD27 deficiency; EBV-induced lymphoproliferation; Hodgkin lymphoma; hemophagocytic lymphohistiocytosis; hypogammaglobulinemia.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Child, Preschool
  • Epstein-Barr Virus Infections / diagnosis
  • Epstein-Barr Virus Infections / genetics*
  • Epstein-Barr Virus Infections / immunology
  • Epstein-Barr Virus Infections / pathology
  • Exome
  • Female
  • Flow Cytometry
  • Heterozygote
  • Hodgkin Disease / diagnosis
  • Hodgkin Disease / genetics*
  • Hodgkin Disease / immunology
  • Hodgkin Disease / pathology
  • Homozygote
  • Humans
  • Immunophenotyping
  • Infant
  • Lymphohistiocytosis, Hemophagocytic / diagnosis
  • Lymphohistiocytosis, Hemophagocytic / genetics*
  • Lymphohistiocytosis, Hemophagocytic / immunology
  • Lymphohistiocytosis, Hemophagocytic / pathology
  • Lymphoproliferative Disorders / diagnosis
  • Lymphoproliferative Disorders / genetics*
  • Lymphoproliferative Disorders / immunology
  • Lymphoproliferative Disorders / pathology
  • Male
  • Mutation*
  • Tumor Necrosis Factor Receptor Superfamily, Member 7 / deficiency
  • Tumor Necrosis Factor Receptor Superfamily, Member 7 / genetics*
  • Tumor Necrosis Factor Receptor Superfamily, Member 7 / immunology
  • Uveitis / diagnosis
  • Uveitis / genetics*
  • Uveitis / immunology
  • Uveitis / pathology
  • Young Adult

Substances

  • Tumor Necrosis Factor Receptor Superfamily, Member 7