Pharmacologic studies in vulnerable populations: Using the pediatric experience

Semin Perinatol. 2015 Nov;39(7):532-6. doi: 10.1053/j.semperi.2015.08.007. Epub 2015 Sep 8.

Abstract

Historically, few data exist to guide dosing in children and pregnant women. Multiple barriers to inclusion of these vulnerable populations in clinical trials have led to this paucity of data. However, federal legislation targeted at pediatric therapeutics, innovative clinical trial design, use of quantitative clinical pharmacology methods, pediatric thought leadership, and collaboration have successfully overcome many existing barriers. This success has resulted in improved knowledge on pharmacokinetics, safety, and efficacy of therapeutics in children. To date, research in pregnant women has not been characterized by similar success. Wide gaps in knowledge remain despite the common use of therapeutics in pregnancy. Given the similar barriers to drug research and development in pediatric and pregnant populations, the route toward success in children may serve as a model for the advancement of drug development and appropriate drug administration in pregnant women.

Keywords: children; drug development; drug trials; pregnancy.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, N.I.H., Intramural
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.
  • Review

MeSH terms

  • Adult
  • Child
  • Child, Preschool
  • Clinical Trials as Topic
  • Cooperative Behavior
  • Dosage Forms
  • Drug Administration Routes
  • Female
  • Humans
  • Infant
  • Infant, Newborn
  • Male
  • Maternal-Fetal Exchange
  • Off-Label Use
  • Pediatrics*
  • Pregnancy
  • Pregnant Women*
  • Prescription Drugs / pharmacokinetics*
  • United States
  • United States Food and Drug Administration*
  • Vulnerable Populations

Substances

  • Dosage Forms
  • Prescription Drugs